Events | Patient Education | American Society of Gene & Cell Therapy ASGCT |

<!DOCTYPE html> <html xmlns="http://www.w3.org/1999/xhtml"> <head>  <script type="text/javascript">(function (w, d, s, l, i) { w[l] = w[l] || []; w[l].push({ 'gtm.start': new Date().getTime(), event: 'gtm.js' }); var f = d.getElementsByTagName(s)[0], j = d.createElement(s), dl = l != 'dataLayer' ? '&l=' + l : ''; j.async = true; j.src = 'https://www.googletagmanager.com/gtm.js?id=' + i + dl; f.parentNode.insertBefore(j, f); })(window, document, 'script', 'dataLayer', 'GTM-NFW5DS9');</script>   <script type="text/javascript"> //------------------------------------------------------- var z_account = "2632C1D8-6432-4D3A-93D6-08AAECC53F86"; var z_collector = "asgct.informz.net"; var z_cookieDomain = ".asgct.org"; //------------------------------------------------------- (function (e, o, n, r, t, a, s) { e[t] || (e.GlobalSnowplowNamespace = e.GlobalSnowplowNamespace || [], e.GlobalSnowplowNamespace.push(t), e[t] = function () { (e[t].q = e[t].q || []).push(arguments) }, e[t].q = e[t].q || [], a = o.createElement(n), s = o.getElementsByTagName(n)[0], a.async = 1, a.src = r, s.parentNode.insertBefore(a, s)) }(window, document, "script", "https://cdn.informz.net/web_trk/sp.js", "informz_trk")), informz_trk("newTracker", "infz", z_collector + "/web_trk/collector/", { appId: z_account, cookieDomain: z_cookieDomain }), informz_trk("setUserIdFromLocation", "_zs"), informz_trk("enableActivityTracking", 30, 15); informz_trk("trackPageView", null); </script>  <meta charset="utf-8" /> <meta http-equiv="X-UA-Compatible" content="IE=edge" /> <meta name="viewport" content="width=device-width,user-scalable=no,maximum-scale=1.0,initial-scale=1.0" /> <link href="/BlueKey/pe_assets/build/styles.css" rel="stylesheet" /> <script type="text/javascript" defer="defer" src="https://extend.vimeocdn.com/ga/127349852.js"></script> <meta name="twitter:card" content="summary_large_image" /> <meta name="twitter:site" content="https://twitter.com/ASGCTherapy" <meta name="twitter:creator" content="@ASGCTherapy" <meta name="twitter:title" content="Lunch & Learn: Gene Therapy for SMA" <meta name="twitter:image" content="~00000000-0000-0000-0000-000000000000/attachment.aspx" <meta charset="UTF-8" /> <link href="/App_Themes/Default/Images/favicon.ico" type="image/x-icon" rel="shortcut icon" /> <link href="/App_Themes/Default/Images/favicon.ico" type="image/x-icon" rel="icon" /> <title> Events | Patient Education | American Society of Gene & Cell Therapy ASGCT | </title></head> <body class="LTR IE IE7 ENUS ContentBody">  <noscript><iframe src="https://www.googletagmanager.com/ns.html?id=GTM-NFW5DS9" height="0" width="0" style="display:none;visibility:hidden"></iframe></noscript>  <form method="post" action="/events/lunch-learn-gene-therapy-for-sma" id="aspnetForm"> <div class="aspNetHidden"> <input type="hidden" name="__CMSCsrfToken" id="__CMSCsrfToken" value="jKoKu/kVYzX7im+eeQMF/isJWLoZJr29tRC0vOfhzmjhg+SKLBR3mbC19e3w5fZly8drcdTku5bJ+WDlGURIXAJ8kf0=" /> <input type="hidden" name="__EVENTTARGET" id="__EVENTTARGET" value="" /> <input type="hidden" name="__EVENTARGUMENT" id="__EVENTARGUMENT" value="" /> <input type="hidden" name="__VIEWSTATE" id="__VIEWSTATE" value="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" /> </div> <script type="text/javascript"> //<![CDATA[ var theForm = document.forms['aspnetForm']; if (!theForm) { theForm = document.aspnetForm; } function __doPostBack(eventTarget, eventArgument) { if (!theForm.onsubmit || (theForm.onsubmit() != false)) { theForm.__EVENTTARGET.value = eventTarget; theForm.__EVENTARGUMENT.value = eventArgument; theForm.submit(); } } //]]> </script> <script src="/WebResource.axd?d=UZQNzmZXG1IdUaHxtavOjRvGEvOmz1kvw97PqEaxzBy7Ys-tUotw-RqgdbsvC3g_7cXjehqAdA_N6kbuK73WBAVGdxo1&t=638562384440000000" type="text/javascript"></script> <input type="hidden" name="lng" id="lng" value="en-US" /> <script type="text/javascript"> //<![CDATA[ function PM_Postback(param) { if (window.top.HideScreenLockWarningAndSync) { window.top.HideScreenLockWarningAndSync(1080); } if(window.CMSContentManager) { CMSContentManager.allowSubmit = true; }; __doPostBack('ctl00$CMSPortalManager1$am',param); } function PM_Callback(param, callback, ctx) { if (window.top.HideScreenLockWarningAndSync) { window.top.HideScreenLockWarningAndSync(1080); }if (window.CMSContentManager) { CMSContentManager.storeContentChangedStatus(); };WebForm_DoCallback('ctl00$CMSPortalManager1$am',param,callback,ctx,null,true); } //]]> </script> <script src="/ScriptResource.axd?d=WTJtoz6EJe-loUBJ9stbRxqzgpVp8oo0KdZGkhGfcu6Lr7kb5LeNfx21FKi8mxEL1oDZOLAxiAqERpClgBx-A6lZ0DJ1qKcDZB1NuIbRd8o9S7aG0&t=7c776dc1" type="text/javascript"></script> <script src="/ScriptResource.axd?d=y6KGkkRaceYF_mkApXCXMQ_rMQVX59BlJ-ut-lQDHw88bR5bbS86epdVNwimj01duE6_OophLX4sBTOgb8_5dNLaY2Mx5DHMJj7Rbr4kPMV1-AOS5VF5-QEC8oG-_-aHoWoyqA2&t=7c776dc1" type="text/javascript"></script> <script type="text/javascript"> //<![CDATA[ var CMS = CMS || {}; CMS.Application = { "isDialog": false, "isDebuggingEnabled": false, "applicationUrl": "/", "isRTL": "false", "imagesUrl": "/CMSPages/GetResource.ashx?image=%5bImages.zip%5d%2f" }; //]]> </script> <div class="aspNetHidden"> <input type="hidden" name="__VIEWSTATEGENERATOR" id="__VIEWSTATEGENERATOR" value="AD1448C3" /> <input type="hidden" name="__EVENTVALIDATION" id="__EVENTVALIDATION" value="/wEdAAOL7jK6j5a6/bONyw/EYK2pDMN6QAizBz4KoPbUd79oAZD1NQdfl/cWuar5Vh7dGPSrEeBXEyL8aUASsIs58vhostrBXg==" /> </div> <script type="text/javascript"> //<![CDATA[ Sys.WebForms.PageRequestManager._initialize('ctl00$manScript', 'aspnetForm', ['tctl00$ctxM',''], [], [], 90, 'ctl00'); //]]> </script> <div id="ctl00_ctxM"> </div> <header class="c-header"> <a href="#content" class="show-on-focus">Skip to main content</a> <div class="c-header-utilities"> <div class="container"> <div class="columns is-vcentered"> <div class="column"> <a href="https://asgct.org" class="is-external">ASGCT.org</a> </div> <div class="column is-half"> <a href="/"> <div class="c-header-images"> <div class="c-header-image"> <img src="/PatientEducation/media/PatientEducation/ASGCT_Web_Horz_Navy.png?ext=.png" alt="" /> </div> <div class="c-header-image"> <img src="/PatientEducation/media/PatientEducation/temp-pe-logo.png?ext=.png" alt="Patient Education Logo" /> </div> </div> </a> </div>  <div class="column"> <div class="c-header-search"> <div class="c-header-search-wrap"> <input name="keyword" type="text" id="searchtext" placeholder="Search" aria-required="false" /> <label for="searchtext" class="is-sr-only">Keyword search</label> <button type="button" data-encode="searchtext" data-path="/search-results" data-query="searchtext"> <span class="is-sr-only">Search</span> <span class="c-search-icon"></span> </button> </div> </div> </div> </div> </div> </div> <div class="c-header-utilities-mobile"> <div class="c-header-images"> <div class="c-header-image"> <a href="https://asgct.org" class="is-external"><img src="/PatientEducation/media/PatientEducation/ASGCT_Web_Horz_Navy.png?ext=.png" alt="" /></a> </div> <div class="c-header-image"> <a href="/"><img src="/PatientEducation/media/PatientEducation/temp-pe-logo.png?ext=.png" alt="Patient Education Logo" /></a> </div> </div> <button class="c-nav-toggle" type="button" aria-controls="c-nav-main" aria-expanded="false" data-togglevisibility="data-togglevisibility"> <p class="is-sr-only">Open Navigation</p> <p class="is-sr-only" aria-hidden="true">Close Navigation</p> <span class="c-nav-toggle-menu"></span> </button> </div> <div id="ctl00_plcMain_bkSiteHeader_headerBanner"> <div class="header-alert"> <div class="container"> <p id="ctl00_plcMain_bkSiteHeader_pBanner"><b><a href="https://patienteducation.asgct.org/newsletter/subscribe-to-the-patient-press">Subscribe today to ASGCT's patient-centered newsletter, The Patient Press!</a></b></p> </div> </div> </div> <nav class="c-nav-main" id="c-nav-main" aria-hidden="true"> <div class="container"> <div class="c-header-search is-hidden-desktop"> <div class="c-header-search-wrap"> <input name="" type="text" id="global-search" placeholder="Search" aria-required="false" /> <label for="global-search" class="is-sr-only">Keyword search</label> <button type="button" data-encode="global-search" data-path="/search-results" data-query="searchtext"> <span class="is-sr-only">Search</span> <span class="c-search-icon"></span> </button> </div> </div> <ul> <li> <a href="/gene-therapy-101">Gene & Cell Therapy 101</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/gene-therapy-101/gene-therapy-basics">Gene Therapy Basics</a> </li> <li> <a href="/gene-therapy-101/cell-therapy-basics">Cell Therapy Basics</a> </li> <li> <a href="/gene-therapy-101/gene-therapy-approaches">Gene Therapy Approaches</a> </li> <li> <a href="/gene-therapy-101/gene-editing">Gene Editing</a> </li> <li> <a href="/gene-therapy-101/clinical-trials">Clinical Trials</a> </li> <li> <a href="/gene-therapy-101/vectors-101">Vectors 101</a> </li> <li> <a href="/gene-therapy-101/glossary">Glossary</a> </li> <li> <a href="/gene-therapy-101/covid19-vaccines">COVID-19</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/disease-treatments">Condition Treatments</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/disease-treatments/fda-approved-cell-gene-therapy-products">FDA-Approved Cell & Gene Therapy Products</a> </li> <li> <a href="/disease-treatments/batten">Batten Disease</a> </li> <li> <a href="/disease-treatments/blood-disorders">Beta Thalassemia & Other Blood Disorders</a> </li> <li> <a href="/disease-treatments/leukodystrophy">CALD and MLD</a> </li> <li> <a href="/disease-treatments/car-t-basics">CAR-T Basics</a> </li> <li> <a href="/disease-treatments/fabry">Fabry Disease</a> </li> <li> <a href="/disease-treatments/gaucher-disease">Gaucher Disease</a> </li> <li> <a href="/disease-treatments/gm1-gangliosidosis">GM1 Gangliosidosis</a> </li> <li> <a href="/disease-treatments/gm2-tay-sachs-sandhoff">Tay-Sachs and Sandhoff Disease</a> </li> <li> <a href="/disease-treatments/hemophilia">Hemophilia</a> </li> <li> <a href="/disease-treatments/huntingtons-disease">Huntington's Disease</a> </li> <li> <a href="/disease-treatments/inherited-retinal-diseases">Inherited Retinal Diseases</a> </li> <li> <a href="/disease-treatments/mps">Mucopolysaccharidoses (MPS)</a> </li> <li> <a href="/disease-treatments/muscular-dystrophy">Muscular Dystrophy</a> </li> <li> <a href="/disease-treatments/pompe-disease">Pompe Disease</a> </li> <li> <a href="/disease-treatments/parkinsons-disease">Parkinson's Disease</a> </li> <li> <a href="/disease-treatments/sickle-cell-disease">Sickle Cell Disease</a> </li> <li> <a href="/disease-treatments/sma">Spinal Muscular Atrophy</a> </li> <li> <a href="/disease-treatments/wilson-disease">Wilson Disease</a> </li> <li> <a href="/disease-treatments/xlmtm">X-Linked Myotubular Myopathy</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/patient-journey">Patient Journey</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/patient-journey/identifying-a-genetic-disease">Identifying a Genetic Disease</a> </li> <li> <a href="/patient-journey/next-steps-with-a-diagnosis">Next Steps With a Diagnosis</a> </li> <li> <a href="/patient-journey/patient-focused-policy-positions">Patient-Focused Policy Positions</a> </li> <li> <a href="/patient-journey/stimulating-research">Stimulating Research</a> </li> <li> <a href="/patient-journey/considering-a-clinical-trial">Considering a Clinical Trial</a> </li> <li> <a href="/patient-journey/ethical-issues-germline-gene-editing">Ethical Issues: Germline Gene Editing</a> </li> <li> <a href="/patient-journey/ethical-issues-illegitimate-clinical-trials">Ethical Issues: Unproven Stem Cell Products</a> </li> <li> <a href="/patient-journey/gene-therapy-centers">Gene Therapy Centers</a> </li> <li> <a href="/patient-journey/clinical-trials-finder">Clinical Trials Finder</a> </li> <li> <a href="/patient-journey/on-demand">On Demand Webinars</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/newsletter">Newsletter</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/newsletter/subscribe-to-the-patient-press">Subscribe to The Patient Press</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/quick-takes">Quick Takes</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/quick-takes/focused-ultrasound-in-cell-and-gene-therapies">Focused Ultrasound in CGTs</a> </li> <li> <a href="/quick-takes/access-to-approved-cell-and-gene-therapies">Access to Approved CGTs</a> </li> <li> <a href="/quick-takes/informed-consent">Informed Consent</a> </li> <li> <a href="/quick-takes/state-of-the-field-cgt-highlights-and-approvals-20">State of the Field: CGT Highlights and Approvals of 2023</a> </li> <li> <a href="/quick-takes/genetic-testing-and-clinical-trial-eligibility">Genetic Testing and Clinical Trial Eligibility</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/events">Events</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/events/empowering-patients-2025-a-cell-and-gene-therapies">Empowering Patients 2025: A Cell and Gene Therapies Summit</a> </li> <li> <a href="/events/annual-meeting-patient-advocate-offerings">Annual Meeting-Patient Advocate Offerings</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/about-asgct">About</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/about-asgct/overview">Overview</a> </li> <li> <a href="/about-asgct/about-asgct">About ASGCT</a> </li> <li> <a href="/about-asgct/news">ASGCT News</a> </li> <li> <a href="/about-asgct/privacy-policy">Privacy Policy</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/support">Support</a> </li> </ul> <a href="asgct.org" class="px-1 is-external is-hidden-desktop">ASGCT.org</a> </div> </nav> </header> <main class="c-main" id="content"> <section class="c-breadcrumbs"> <div class="container"> <span><a href="/">Home</a> > </span> <a href="/events" title="Events" class="CMSBreadCrumbsLink">Events</a> </div> </section> <section class="section"> <div class="container"> <div class="columns"> <div class="column is-8"> <h1 class="is-like-h2">Lunch & Learn: Gene Therapy for SMA</h1> </div> </div> <div class="columns"> <div class="column is-8"> <div class="c-leader"> </div> <figure id="ctl00_plcMain_rptContent_ctl00_figure" class="c-leader-image"> <img src="" alt="" /> </figure> <div class="content mb-6"> <p><iframe allow="accelerometer; autoplay; clipboard-write; encrypted-media; gyroscope; picture-in-picture" allowfullscreen="" frameborder="0" height="315" src="https://www.youtube.com/embed/YFEMR1ZHYFc" title="YouTube video player" width="560"></iframe></p> <p><a href="https://patienteducation.asgct.org/disease-treatments/sma" target="_blank">Spinal Muscular Atrophy</a> (SMA) is a rare genetic disease that affects the motor nerve cells in the spinal cord and is the leading genetic cause of infant mortality. During this education session, caregivers will learn from experienced clinicians who will share insights on gene therapy options for SMA as well as a parent's perspective on having a child receive approved treatments. Presentations will be followed by a Q&A for attendees. This event is cohosted by <a href="https://www.fightingforkaiden.org/" target="_blank">Fighting for Kaiden Foundation</a>, <a href="https://www.laughingatmynightmare.com/" target="_blank">Laughing at My Nightmare</a>, and <a href="https://asgct.org/" target="_blank">ASGCT</a>.</p> <h2>Agenda</h2> <p><strong>Introduction</strong><br /> 11 – 11:05 a.m. <br /> ASGCT Welcome – Ali Kujawski, MPH <br /> Laughing at My Nightmare – Laura Burcaw<br /> Fighting for Kaiden – Kelly Eakin  </p> <p><strong>Understanding Gene Therapy and Treatment</strong><br /> 11:05 – 11:20 a.m. <br /> Speaker: <strong>Megan Waldrop, MD</strong>, Nationwide Children’s Hospital and Ohio State University </p> <p>This talk will introduce FDA-approved treatment options: how they work, how they are given, and eligibility considerations. There will be a review of some of the active clinical trials to understand dual treatments and expanding indications. The different pathways to access these treatments will also be discussed, including the role of newborn screenings, accessing approved therapies, and participating in a clinical trial. </p> <p><strong>Caregiver Considerations </strong> <br /> 11:20 – 11:35 a.m. <br /> Speaker: <strong>Susan Iannaccone, MD, FAAN</strong>, UT Southwestern Medical Center </p> <p>This talk will address risks and benefits of gene therapy, along with current outcomes for asymptomatic versus symptomatic individuals. There will also be guidance on how to decide which option is best for your child.  </p> <p><b>A Parent's Experience</b><br /> 11:35 – 11:45 a.m. <br /> Speaker: <b>Brian Council</b></p> <p>Brian will share his family’s experience from an SMA diagnosis to his daughter receiving all three of the approved treatments. He will discuss what led his family down each treatment path and what lessons they learned along the way.</p> <p><strong>Moderated Q&A</strong><br /> 11:45 a.m. – 12:00 p.m.  </p> <h2>Cohosted by:</h2> <p><img alt="" src="https://asgct.org/ASGCT/media/about/Screenshot-(409).png" /></p> </div> </div> <div class="column is-4 pl-4"> <div class="c-nav-local-wrap"> <div class="asideBox"> <h3> Related Pages</h3> <hr class="is-secondary" /> <ul class="c-nav-local-list"> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/empowering-patients-2025-a-cell-and-gene-therapies">Empowering Patients 2025: A Cell and Gene Therapies Summit</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/april-lunch-learn-intro-to-non-viral-vectors">Lunch & Learn: Intro to Non-Viral Vectors</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-learn-recently-approved-therapies">Feb. Lunch & Learn: Recently Approved Therapies</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-learn-roadblocks-to-developing-a-treatment">March Lunch & Learn: Roadblocks to Developing a Treatment</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-learn-meet-the-patients">Lunch & Learn: Meet the Patients</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-and-learn-navigating-patient-provider-conver">Lunch & Learn: Navigating the Patient-Provider Conversation</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-and-learn-meet-the-researchers">Lunch and Learn: Meet the Researchers</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-and-learn-pathway-to-approval">Lunch & Learn: The Pathway to Approval</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/schedule">Schedule</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/webinars">Partnered Webinars</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/august-25-routes-of-administration">Lunch & Learn: Routes of Administration</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-learn-preclinical-studies">Lunch & Learn: Diving into Preclinical Studies</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-learn-annual-meeting-research">Lunch & Learn: Annual Meeting Research Highlights</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/register-what-to-expect-as-a-participant-in-a-gene">Register: What to Expect as a Participant in a Gene Therapy Clinical Trial</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-learn-aav-vectors">Lunch & Learn: How AAV Vectors Are Made</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-learn-viral-vectors">Lunch & Learn: Intro to Viral Vectors</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/lunch-learn-gene-therapy-101">Lunch & Learn: Gene Therapy 101</a> </li> <li class="c-nav-local-item is-active"><a class="c-nav-local-link" href="/events/lunch-learn-gene-therapy-for-sma">Lunch & Learn: Gene Therapy for SMA</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/2022-lunch-learn-schedule">2022 Lunch & Learn Schedule</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/events/annual-meeting-patient-advocate-offerings">Annual Meeting-Patient Advocate Offerings</a> </li> </ul> </div> </div> </div> </div> </div> <div class="lastUpdatedTag"> <p>Last Updated: 01/30/2024</p> </div> </section> </main> <footer class="c-footer"> <div class="c-footer-primary"> <section class="section"> <div class="container"> <div class="columns"> <div class="column c-footer-section"> <p><img alt="" src="/PatientEducation/media/PatientEducation/logo_white.png" /></p> <p>20800 Swenson Dr., Suite 300<br /> Waukesha, WI 53186</p> </div> <div class="column is-two-fifths c-footer-section"> <ul class="c-utility-list"> <li><a href="#">Gene Therapy 101</a></li> <li><a href="#">Disease Treatments</a></li> <li><a href="#">Clinical Trials</a></li> <li><a href="/patient-journey">Patient Journey</a></li> <li><a href="/about-asgct">About</a></li> <li><a href="/support">Support</a></li> <li><a href="https://asgct.org/about/privacy-policy" target="_blank">Privacy Policy</a></li> </ul> </div> <div class="column c-footer-section"> <h3 class="mb-3">Connect with ASGCT</h3> <p class="mb-0"><span>Phone: 414</span>.278.1341</p> <p><a href="mailto:info@asgct.org">info@asgct.org</a></p> <p> <div class="c-social"> <ul class="c-social-list"> <li class="c-social-item"><a href="https://twitter.com/ASGCTherapy" target="_blank" class="c-social-link twitter"><span class="is-sr-only">Twitter</span></a></li> <li class="c-social-item"><a href="https://www.facebook.com/ASGCTherapy" target="_blank" class="c-social-link facebook"><span class="is-sr-only">Facebook</span></a></li> <li class="c-social-item"><a href="https://www.instagram.com/asgctherapy" target="_blank" class="c-social-link instagram"><span class="is-sr-only">Instagram</span></a></li> <li class="c-social-item"><a href="https://www.linkedin.com/company/asgct" target="_blank" class="c-social-link linkedin"><span class="is-sr-only">LinkedIn</span></a></li> <li class="c-social-item"><a href="https://www.youtube.com/user/ASGCT" target="_blank" class="c-social-link youtube"><span class="is-sr-only">YouTube</span></a></li> </ul> </div> </p> </div> </div> </div> </section> </div> <div class="c-footer-secondary"> <section class="section py-4"> <div class="container"> <div class="columns"> <div class="column"> <p class="is-small">© 2024 All rights reserved. American Society of Gene & Cell Therapy.</p> <p class="is-tiny">Web design by <a href="https://www.reasononeinc.com/kentico" target="_blank">Reason One</a>. Powered by <a href="http://www.kentico.com" target="_blank">Kentico</a>.</p> </div> </div> </div> </section> </div> </footer> <div class="CookieConsent"> <span id="ctl00_cookieLawQ_lblText" class="ConsentText">This site uses cookies to offer you a better user experience and to analyze site traffic. By continuing to use this website, you accept our use of cookies.</span> <span class="ConsentButtons"> <input type="submit" name="ctl00$cookieLawQ$btnAllowSpecific" value="OPT OUT" id="ctl00_cookieLawQ_btnAllowSpecific" class="ConsentButton btn btn-default" /> <input type="submit" name="ctl00$cookieLawQ$btnAllowAll" value="ACCEPT" id="ctl00_cookieLawQ_btnAllowAll" class="ConsentButton btn btn-default" /> </span> </div> <script src="/BlueKey/pe_assets/build/main.js" type="text/javascript"></script> <script type="text/javascript"> //<![CDATA[ var callBackFrameUrl='/WebResource.axd?d=nNME_ObE2oIDm535eYM9xWmIMy-HXBVdo54Ly6sA5tAYPS1aA-gFDzodlP9ijTBRgmjStONrH4-ISuRTp7slHiYkACw1&t=638562384440000000'; WebForm_InitCallback();//]]> </script> </form> </body> </html>

CINXE.COM

Events | Patient Education | American Society of Gene & Cell Therapy ASGCT |