CINXE.COM
Cell and Gene Therapy Center | Rowan Research | Rowan University
<!DOCTYPE html PUBLIC "-//W3C//DTD XHTML+RDFa 1.0//EN" "http://www.w3.org/MarkUp/DTD/xhtml-rdfa-1.dtd"> <html xmlns="http://www.w3.org/1999/xhtml" class="js csstransforms csstransforms3d csstransitions" dir="ltr" version="XHTML+RDFa 1.0" xml:lang="en" xmlns:content="http://purl.org/rss/1.0/modules/content/" xmlns:dc="http://purl.org/dc/terms/" xmlns:foaf="http://xmlns.com/foaf/0.1/" xmlns:og="http://ogp.me/ns#" xmlns:rdfs="http://www.w3.org/2000/01/rdf-schema#" xmlns:sioc="http://rdfs.org/sioc/ns#" xmlns:sioct="http://rdfs.org/sioc/types#" xmlns:skos="http://www.w3.org/2004/02/skos/core#" xmlns:xsd="http://www.w3.org/2001/XMLSchema#"> <head profile="http://www.w3.org/1999/xhtml/vocab"> <!-- Google Tag Manager --> <script>(function(w,d,s,l,i){w[l]=w[l]||[];w[l].push({'gtm.start': new Date().getTime(),event:'gtm.js'});var f=d.getElementsByTagName(s)[0], j=d.createElement(s),dl=l!='dataLayer'?'&l='+l:'';j.async=true;j.src= 'https://www.googletagmanager.com/gtm.js?id='+i+dl;f.parentNode.insertBefore(j,f); })(window,document,'script','dataLayer','GTM-KBS9C8J');</script> <!-- End Google Tag Manager --> <link href="https://www.rowan.edu/_files/_files/css/flexslider.css" media="all" rel="stylesheet" type="text/css" /> <link href="https://www.rowan.edu/_files/_files/css/main.css" media="all" rel="stylesheet" type="text/css" /> <link href="https://www.rowan.edu/_files/_files/css/customglobal.css" media="all" rel="stylesheet" type="text/css" /> <link href="https://www.rowan.edu/_files/_files/css/anniversary.css" media="all" rel="stylesheet" type="text/css" /> <link href="https://www.rowan.edu/_files/_files/css/brightedge.css" media="all" rel="stylesheet" type="text/css" /> <style media="all" type="text/css"> /*<![CDATA[ */ .username-textfield{display:none !important;} /* ]]> */ </style> <!-- Font Awesome 6 Pro Max Kit - w/o v4-shims --> <script src="https://kit.fontawesome.com/3766c69bbc.js" crossorigin="anonymous"></script> <script src="https://www.rowan.edu/_files/_files/js/embed.min.js" ></script> <script type="text/javascript"> setTimeout(function(){var a=document.createElement("script"); var b=document.getElementsByTagName("script")[0]; a.src=document.location.protocol+"//script.crazyegg.com/pages/scripts/0010/6392.js?"+Math.floor(new Date().getTime()/3600000); a.async=true;a.type="text/javascript";b.parentNode.insertBefore(a,b)}, 1); </script> <!--BE IXF: JavaScript begin--> <!--Access to and use of BrightEdge AutoPilot - Self Connecting Pages is governed by the Infrastructure Product Terms located at: www.brightedge.com/infrastructure-product-terms. Customer acknowledges and agrees it has read, understands and agrees to be bound by the Infrastructure Product Terms. --> <script src="//cdn.bc0a.com/autopilot/f00000000251854/autopilot_sdk.js" ></script> <!--BE IXF: JavaScript end--> <meta content="text/html; charset=UTF-8" http-equiv="Content-Type" /> <!--[if IE]> <meta http-equiv="X-UA-Compatible" content="IE=edge,chrome=1" /> <![endif]--> <meta content="yes" name="apple-mobile-web-app-capable" /> <link href="https://www.rowan.edu/_files/_files/images/rowan_logo_torch_152px.png" rel="apple-touch-icon" sizes="152x152" /> <meta content="width=device-width, initial-scale=1.0" name="viewport" /> <link href="https://www.rowan.edu/_files/_files/images/favicon.ico" rel="shortcut icon" type="image/vnd.microsoft.icon" /> <meta content="text/html; charset=UTF-8" http-equiv="Content-Type" /> <!--[if IE]> <meta http-equiv="X-UA-Compatible" content="IE=edge,chrome=1" /> <![endif]--> <meta content="yes" name="apple-mobile-web-app-capable" /> <link href="/_files/_files/images/rowan_logo_torch_152px.png" rel="apple-touch-icon" sizes="152x152" /> <meta content="width=device-width, initial-scale=1.0" name="viewport" /> <link href="/_files/_files/images/favicon.ico" rel="shortcut icon" type="image/vnd.microsoft.icon" /> <link href="https://research.rowan.edu/research-areas/biomedical/leone/index.html" rel="canonical" /> <meta content="A Leader in University Academics" name="description" /> <meta content="Cell and Gene Therapy Center" property="og:title" /> <meta content="website" property="og:type" /> <meta content="https://research.rowan.edu/research-areas/biomedical/leone/index.html" property="og:url" /> <meta content="https://research.rowan.edu/research-areas/biomedical/leone/images/leone-headerimage5.jpg" property="og:image" /> <meta content="@RowanUniversity" name="twitter:site" /> <meta content="summary" name="twitter:card" /> <meta content="https://research.rowan.edu/research-areas/biomedical/leone/index.html" name="twitter:url" /> <meta content="Cell and Gene Therapy Center | Rowan University" name="twitter:title" /> <title>Cell and Gene Therapy Center | Rowan Research | Rowan University</title> </head> <body class="html not-front not-logged-in no-sidebars page-node page-node- page-node-9466 node-type-landing-page domain-rowan-ohodev-com platform-windows domain-rowan"> <!-- Google Tag Manager (noscript) --> <noscript><iframe height="0" src="https://www.googletagmanager.com/ns.html?id=GTM-KBS9C8J" style="display:none;visibility:hidden" width="0" ></iframe></noscript> <!-- End Google Tag Manager (noscript) --> <div id="header"> <div class="container"> <a class="skip-main" href="#main">Skip to main content</a> <div class="top-menu"> <div class="tab"> <div class="personas"><menu> <li><a class="news" href="https://today.rowan.edu/index.html">News</a></li> <li><a class="alumni" href="https://www.alumni.rowan.edu/s/1653/02-alumni/start.aspx?gid=2&pgid=61">Alumni</a></li> <li><a class="parent" href="https://sites.rowan.edu/parentsfamily/index.html">Parents</a></li> <li><a class="donor" href="https://sites.rowan.edu/advancement/index.html">Donors</a></li> <li><a class="jobs" href="https://jobs.rowan.edu/en-us/listing/">Jobs</a></li> <a href="https://admissions.rowan.edu/admissions-process/index.html"><button class="apply-button">Apply</button></a> <a href="https://my.rowan.edu/"><button class="my-rowan"><span class="my">my</span>Rowan</button></a></menu></div> </div> </div> <header> <div class="region region-header clearfix"> <div class="block block-block site-logo site-logo-main" id="block-block-1"> <div class="content"><a href="https://www.rowan.edu/index.html" id="logo" rel="home" title="Home">Rowan University</a></div> </div> <div class="block block-block" id="block-block-13"> <div class="block block-menu-block nav clearfix" id="block-menu-block-1"> <div class="content"> <div class="menu-block-wrapper menu-block-1 menu-name-main-menu parent-mlid-0 menu-level-1"> <ul aria-labelledby="btnNavMenu" class="menu js-dropdown" id="js-nav-main"> <li class="first expanded menu-mlid-512"><a class="parent" href="https://www.rowan.edu/admissions_aid/index.html" id="linkAdmissions">Admissions & Aid</a> <ul class="menu"> <li class="first leaf menu-mlid-2155"><a href="https://admissions.rowan.edu/index.html">First-Year Admissions</a></li> <li class="first leaf menu-mlid-2155"><a href="https://admissions.rowan.edu/admissions-process/transfer-requirements/index.html">Transfer Admissions</a></li> <li class="first leaf menu-mlid-2155"><a href="https://sites.rowan.edu/financial-aid/index.html">Financial Aid</a></li> <li class="first leaf menu-mlid-2155"><a href="https://global.rowan.edu/index.html" rel="noopener noreferrer" target="_blank">Graduate Admissions</a></li> <li class="first leaf menu-mlid-2155"><a href="https://www.rowan.edu/admissions_aid/medical_education.html">Medical Education Admissions</a></li> <li class="first leaf menu-mlid-2155"><a href="https://admissions.rowan.edu/international.html">International Admissions</a></li> <li class="first leaf menu-mlid-2155"><a href="https://apply.rowan.edu/portal/visit" title="Register to visit Rowan University for a Tour or Open House">Tours & Open Houses</a></li> <li class="first leaf menu-mlid-2155"><a href="https://www.rowan.edu/admissions_aid/online_learning.html">Online Learning</a></li> <li class="last leaf menu-mlid-1316"><a href="https://global.rowan.edu/index.html">Degree Completion</a></li> </ul> </li> <li class="expanded menu-mlid-1834"><a class="parent" href="https://www.rowan.edu/academics/index.html" id="linkAcademics">Academics</a> <ul class="menu"> <li class="first leaf has-children menu-mlid-1833"><a href="https://www.rowan.edu/academics/colleges_and_schools/index.html">Colleges & Schools</a></li> <li class="leaf menu-mlid-1835"><a href="https://www.rowan.edu/academics/degree_programs.html">Degrees & Programs</a></li> <li class="leaf menu-mlid-2288"><a href="https://www.rowan.edu/academics/cou_sche_reg.html">Courses, Schedules & Registration</a></li> <li class="leaf menu-mlid-1837"><a href="https://sites.rowan.edu/student-success/index.html">Student Success</a></li> <li class="leaf menu-mlid-1837"><a href="https://sites.rowan.edu/international/index.html">International</a></li> <li class="leaf menu-mlid-2862"><a href="https://global.rowan.edu/alternate-pathways/summer-winter/index.html" rel="noopener noreferrer" target="_blank">Winter & Summer Sessions</a></li> <li class="leaf menu-mlid-4539"><a href="https://global.rowan.edu/alternate-pathways/county-college-partner-schools/index.html" rel="noopener noreferrer" target="_blank">Camden Campus</a></li> <li class="leaf menu-mlid-1324"><a href="https://www.rowan.edu/academics/university_libraries.html">Rowan University Libraries</a></li> <li class="last leaf menu-mlid-1840"><a href="https://www.rowan.edu/academics/bookstore.html">Bookstore</a></li> </ul> </li> <li class="expanded menu-mlid-515"><a class="parent" href="https://www.rowan.edu/campus_life/index.html" id="linkCampusLife">Campus Life</a> <ul class="menu"> <li class="first leaf menu-mlid-1345"><a href="https://www.rowan.edu/campus_life/arts.html">The Arts at Rowan</a></li> <li class="leaf has-children menu-mlid-1841"><a href="https://www.rowan.edu/campus_life/atheletics_sports.html">Athletics & Sports Recreation</a></li> <li class="leaf menu-mlid-1341"><a href="https://www.rowan.edu/campus_life/health_safety.html">Health & Safety</a></li> <li class="leaf menu-mlid-1339"><a href="https://www.rowan.edu/campus_life/housing_dining.html">Housing & Dining</a></li> <li class="leaf menu-mlid-5057"><a href="https://irt.rowan.edu/index.html" rel="noopener noreferrer" target="_blank">Technology on Campus</a></li> <li class="leaf menu-mlid-1843"><a href="https://www.rowan.edu/campus_life/entert_culture.html">Entertainment & Culture</a></li> <li class="last leaf menu-mlid-1843"><a href="https://sites.rowan.edu/center-for-well-being/index.html">Center for Well-being</a></li> </ul> </li> <li class="expanded menu-mlid-1714"><a class="parent" href="https://www.rowan.edu/health_medicine/index.html" id="linkHealth">Health & Medicine</a> <ul class="menu"> <li class="leaf menu-mlid-2077"><a href="https://cmsru.rowan.edu/index.html" rel="noopener noreferrer" target="_blank">Cooper Medical School of Rowan University (MD)</a></li> <li class="last leaf menu-mlid-1708"><a href="https://sites.rowan.edu/vhc/index.html" rel="noopener" target="_blank">Virtua Health College of Medicine & Life Sciences (DO)</a></li> <li class="last leaf menu-mlid-1708"><a href="https://svm.rowan.edu/index.html" rel="noopener noreferrer" target="_blank">Shreiber School of Veterinary Medicine (DVM)</a></li> </ul> </li> <li class="expanded menu-mlid-1720"><a class="parent" href="../../../index.html" id="linkResearch">Research</a> <ul class="menu"> <li class="first leaf menu-mlid-7239"><a href="../../../officeofresearch/index.html">Office of Research</a></li> <li class="leaf menu-mlid-1334"><a href="../../../centers/index.html">Research Centers & Institutes</a></li> <li class="leaf menu-mlid-7240"><a href="http://sjtechpark.org/" rel="noopener" target="_blank">South Jersey Technology Park</a></li> <li class="last leaf menu-mlid-7105"><a href="https://today.rowan.edu/news/topics/research.html">Research News</a></li> </ul> </li> <li class="expanded menu-mlid-756"><a class="" href="https://sites.rowan.edu/military/index.html">Military/Veterans</a></li> <li class="expanded menu-mlid-756"><a href="https://sites.rowan.edu/center-for-well-being/thrive/index.html">Thrive</a></li> <li class="expanded menu-mlid-756"><a class="parent" href="https://www.rowan.edu/about/index.html" id="linkAbout">About</a> <ul class="menu"> <li class="first leaf menu-mlid-1325"><a href="https://www.rowan.edu/about/leadership.html">Leadership</a></li> <li class="leaf has-children menu-mlid-564"><a href="https://www.rowan.edu/about/oppaf/index.html">Our Past, Present & Future</a></li> <li class="leaf has-children menu-mlid-1147"><a href="https://www.rowan.edu/about/visiting/index.html">Visiting Rowan</a></li> <li class="leaf menu-mlid-761"><a href="https://www.rowan.edu/about/working.html">Working at Rowan</a></li> <li class="leaf menu-mlid-761"><a href="https://sites.rowan.edu/fastfacts/index.html">Rowan Fast Facts</a></li> <li class="leaf menu-mlid-1848"><a href="https://www.rowan.edu/about/giving.html">Giving to Rowan</a></li> <li class="leaf menu-mlid-1424"><a href="https://today.rowan.edu/index.html">News & Events</a></li> <li class="last leaf menu-mlid-1148"><a href="https://www.rowan.edu/about/contact.html">Contact Us</a></li> </ul> </li> </ul> </div> </div> </div> <div class="block block-search" id="block-search-form"><!--<img id="search-toggle" src="data:image/png;base64,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" alt="Search Rowan" />--><button aria-controls="searchForm" aria-expanded="false" class="title toggle-menu" data-menu="#block-search-form .content">Search</button> <div aria-label="Search" class="content js-dropdown" id="searchForm"> <div class="directory"><span class="search-tab"><a href="#edit-search-block-form--2">Search Rowan</a></span><span class="people"><a class="directory" href="https://directory.rowan.edu/">Search People</a></span></div> <form accept-charset="UTF-8" action="//search.rowan.edu/search" class="google-cse-oho" id="search-block-form" method="get"> <div> <div class="container-inline"> <div class="form-item form-type-textfield form-item-search-block-form"><label class="element-invisible" for="edit-search-block-form--2">Search</label> <input class="form-text" id="edit-search-block-form--2" maxlength="128" name="q" placeholder="enter search terms" size="15" title="Enter the terms you wish to search for." type="text" value="" /></div> <div class="form-actions form-wrapper" id="edit-actions"><input class="form-submit" id="edit-submit" name="op" type="submit" value="Go" /></div> <input name="proxystylesheet" type="hidden" value="default_frontend" /> <input name="client" type="hidden" value="default_frontend" /></div> </div> </form></div> </div> </div> </div> </header> </div> <!-- /.container --> </div> <!-- /#header --> <div id="page"> <div class="row container" id="main"> <div class="inner"> <div class="nine columns push-three" id="content"> <h1 class="title hide-tab-desktop" id="page-title">Cell and Gene Therapy Center</h1> <div id="content-top"> <div class="flexslider" id="heroSlider"> <ul class="slides"> <li> <img alt="Cell and Gene Therapy" src="images/leone-headerimage5.jpg" /> <div class="flex-caption"> <p>Cell and Gene Therapy Center</p> </div> </li> <li> <img alt="Cell and Gene Therapy" src="images/leone-headerimage6.jpg" /> <div class="flex-caption"> <p>Cell and Gene Therapy Center</p> </div> </li> <li> <img alt="Cell and Gene Therapy Center" src="images/leone-headerimage8.jpg" /> <div class="flex-caption"> <p>Cell and Gene Therapy Center</p> </div> </li> <li> <img alt="Cell and Gene Therapy Center" src="images/leone-headerimage10.jpg" /> <div class="flex-caption"> <p>Cell and Gene Therapy Center</p> </div> </li> <li> <img alt="Cell and Gene Therapy Center" src="images/leone-headerimage9.jpg" /> <div class="flex-caption"> <p>Cell and Gene Therapy Center</p> </div> </li> </ul> </div> </div> <!-- /#content-top --> <div id="breadcrumb"> <div class="breadcrumb"> <a href="https://www.rowan.edu/"> Rowan University </a> » <a href="../../../index.html"> Rowan Research & Innovation </a> » <a href="../../index.html">Academic Research</a> » <a href="../index.html">Biomedical Science</a> » <a href="index.html">Cell and Gene Therapy Center</a> </div> </div> <h1 class="title hide-tab-mobile" id="page-title">Cell and Gene Therapy Center</h1> <div class="tabs" ></div> <div class="region region-content clearfix"> <div class="block block-system" id="block-system-main"> <div class="content"> <div class="field field-name-body field-type-text-with-summary field-label-hidden clearfix"> <div class="field-items"> <div class="field-item even" property="content:encoded"> <h2>Welcome to the Cell and Gene Therapy Center</h2> <img alt="accentbar.jpg" class="expand-img" height="100%" src="images/accentbar.jpg" style="width: 100%;" width="100%" /> <p>Our laboratory, under the direction of Dr. Paola Leone, studies pediatric white matter diseases and characterizes mechanisms to repair white matter with the goal to prevent and treat disease in patients. Our work focuses on neurological diseases that can be treated using the latest gene transfer technologies and cell transplantation methods. You can learn more by watching the video below or our award-winning film, <a href="https://www.youtube.com/watch?time_continue=6&v=bKmNKo2cAQg" rel="noopener" target="_blank"><strong><em>Little Heroes</em></strong></a>. </p> </div> </div> </div> <div class="field field-name-field-new-flexboxes field-type-entityreference field-label-hidden"> <div class="newCards entity entity-flexbox-container flexbox-container-flexbox-container flexbox-container-style-featured-row flexbox-style-lmr clearfix"> <div class="content"> <div class="field field-name-field-flexbox-ref field-type-entityreference field-label-hidden"> <div class="field-items"> <div class="field-item even"> <div class="entity entity-flexbox flexbox-flexbox clearfix" style="min-height: auto"> <div class="content"> <a href="https://www.youtube.com/watch?time_continue=6&v=bKmNKo2cAQg" target="_blank"> <div class="field field-name-field-flexbox-image field-type-image field-label-hidden"> <img alt="little heroes" src="images/littleheroes-flex.jpg" typeof="foaf:Image" /> </div> </a> <div class="field field-name-field-flexbox-body field-type-text-long field-label-hidden"> <div class="field-items"> <div class="field-item even"> <a href="https://www.youtube.com/watch?time_continue=6&v=bKmNKo2cAQg" target="_blank"> <h2 class="title"><span>Watch our Award-Winning Video</span></h2> </a> <p><p><em>Little Heroes</em> – Winner: Fan Favorite Award<br />Neuro Film Festival, American Academy of Neurology 2013</p></p> </div> </div> </div> </div> </div> </div> <div class="field-item odd"> <div class="entity entity-flexbox flexbox-flexbox clearfix" style="min-height: auto"> <div class="content"> <a href="staff.html" target="_blank"> <div class="field field-name-field-flexbox-image field-type-image field-label-hidden"> <img alt="" src="images/leone-flex3.jpg" typeof="foaf:Image" /> </div> </a> <div class="field field-name-field-flexbox-body field-type-text-long field-label-hidden"> <div class="field-items"> <div class="field-item odd"> <a href="staff.html" target="_blank"> <h2 class="title"><span>Dr. Leone & Staff</span></h2> </a> <p>Dr. Leone's research interests include in vivo neurochemistry of epilepsy and gene transfer approaches for the treatment of neurological disorders. Learn more about Dr. Leone and her researchers.</p> </div> </div> </div> </div> </div> </div> </div> </div> </div> </div> <div class="flexbox-style-text-links clearfix" style="margin-bottom: 30px"> <h2>Support our Work</h2> <img alt="accentbar.jpg" class="expand-img" height="100%" src="images/accentbar.jpg" style="width: 100%;" width="100%" /> <p>We need your help to continue making real advances in treatment of Canavan disease and related brain conditions. Learn more about our research through this video and consider making a donation.</p> <p style="text-align: right;"><a href="https://securelb.imodules.com/s/1653/general/foundation.aspx?sid=1653&gid=2&pgid=644&cid=1486&dids=659" rel="noopener" target="_blank">Donate to the Cell and Gene Therapy Center</a></p> <p> </p> <style><!-- .video-container { position: relative; padding-bottom: 56.25%; padding-top: 30px; height: 0; overflow: hidden; } .video-container iframe, .video-container object, .video-container embed { position: absolute; top: 0; left: 0; width: 100%; height: 100%; } --></style> <div class="video-container"><iframe allowfullscreen="allowfullscreen" height="100%" src="//www.youtube.com/embed/Jxi2X3NKYGI" width="100%" ></iframe></div> </div> <script type="text/javascript">var carouselCount = 1;</script> </div> </div> </div> </div> </div> <!--/#content --> <div class="three columns pull-nine tablet-cols-1 portrait-bottom" id="sidebar-first"> <div id="sidebar-first-nav"> <div class="region region-sidebar-first-nav clearfix"> <div class="block block-views clearfix" id="block-views-landing-pages-block"> <div class="content" id=""> <div class="view view-landing-pages view-id-landing_pages view-display-id-block graphic-title view-dom-id-2281b9fc2406e95eb1bb71f50e7ccd0e"> <div class="view-content"> <div class="views-row views-row-1 views-row-odd views-row-first views-row-last"> <div> <div><h1 class="field field-name-field-overlay-page-title field-type-text field-label-hidden">Cell and Gene Therapy Center</h1> </div> </div> </div> </div> </div> </div> </div> <div class="block block-rowan-stock back-to-link" id="block-rowan-stock-rowan-back-to"> <div class="content"> <a href="../../index.html">Back to Academic Research</a> </div> </div> <div class="block block-menu-block block-og-menu nav-sidebar" id="block-menu-block-4 block-og-menu-og-single-menu-block"> <div class="content"> <div class="menu-block-wrapper menu-block-4 menu-name-main-menu parent-mlid-0 menu-level-2"> <a class="hide-on-desktop show-on-tablet toggle-sidebar" href="../../../index.html">Main Menu</a> <ul class="menu"> <li class="leaf active-trail"><a href="index.html">Cell and Gene Therapy Center</a> </li> <li class="leaf"><a href="about.html">About Us</a> </li> <li class="leaf"><a href="staff.html">Faculty and Staff</a> </li> <li class="leaf"><a href="research.html">Research</a> </li> <li class="leaf"><a href="contact.html">Contact Us</a> </li> </ul> </div> </div> </div> </div> </div> <!-- /#sidebar-first-nav --> <div id="sidebar-first-mid"> <div class="region region-sidebar-first-mid clearfix"> <div class="block block-block" id="block-block-11"> <div class="content"> </div> </div> </div> </div> <!-- /#sidebar-first-mid --> </div> <!-- /#sidebar-first --> </div> <!-- /.inner --> </div> <!-- /#main /.row --> </div> <!-- /#page /.container --> <div class="bottom-full"> <div class="region region-content-bottom-full-width clearfix"> <div class="block block-views" id="block-views-bottom-blocks-block-3"> <div class="content"> <div class="view view-bottom-blocks view-id-bottom_blocks view-display-id-block_3 view-dom-id-7587a1aac78ba4489e40e95558db37b8"> <div class="view-content"> <div class="views-row views-row-1 views-row-odd views-row-first views-row-last" ></div> </div> </div> </div> </div> <div class="block block-views" id="block-views-bottom-blocks-block-12"> <div class="content"> <div class="view view-bottom-blocks view-id-bottom_blocks view-display-id-block_12 view-dom-id-097cb94eb5e5165be8b8fce630faef8f"> <div class="view-content"> <div class="views-row views-row-1 views-row-odd views-row-first views-row-last" ></div> </div> </div> </div> </div> <div class="block block-views" id="block-views-bottom-blocks-block-13"> <div class="content"> <div class="view view-bottom-blocks view-id-bottom_blocks view-display-id-block_13 view-dom-id-c4f39388fd008da322ce59be860b45ce"> <div class="view-content"> <div class="views-row views-row-1 views-row-odd views-row-first views-row-last" ></div> </div> </div> </div> </div> <div class="block block-views" id="block-views-bottom-blocks-block-8"> <div class="content"> <div class="view view-bottom-blocks view-id-bottom_blocks view-display-id-block_8 view-dom-id-944491960f59046f7946173d197e3f89"> <div class="view-content"> <div class="views-row views-row-1 views-row-odd views-row-first views-row-last" ></div> </div> </div> </div> </div> <div class="block block-views" id="block-views-bottom-blocks-block-10"> <div class="content"> <div class="view view-bottom-blocks view-id-bottom_blocks view-display-id-block_10 view-dom-id-bf3e9e8580bc2cbef6395df38c3d8ebe"> <div class="view-content"> <div class="views-row views-row-1 views-row-odd views-row-first views-row-last" ></div> </div> </div> </div> </div> <div class="block block-views" id="block-views-bottom-blocks-block-9"> <div class="content"> <div class="view view-bottom-blocks view-id-bottom_blocks view-display-id-block_9 view-dom-id-f6565e67a268f4ff22862c5341729642"> <div class="view-content"> <div class="views-row views-row-1 views-row-odd views-row-first views-row-last" ></div> </div> </div> </div> </div> <div class="block block-views" id="block-views-bottom-blocks-block-11"> <div class="content"> <div class="view view-bottom-blocks view-id-bottom_blocks view-display-id-block_11 view-dom-id-7c38bdce87958682b75f8641476fa306"> <div class="view-content"> <div class="views-row views-row-1 views-row-odd views-row-first views-row-last" ></div> </div> </div> </div> </div> </div> </div> <div class="clearfix" id="footer"> <footer><div class="container"> <div class="region region-footer clearfix"> <div class="block block-block" id="block-block-2"> <div class="content"> <ul class="social-media"> <li class="twitter"><a href="https://twitter.com/RowanUniversity">Rowan on Twitter</a></li> <li class="facebook"><a href="https://www.facebook.com/RowanUniversity">Rowan on Facebook</a></li> <li class="instagram"><a href="https://www.instagram.com/rowanuniversity/">Rowan on Instagram</a></li> <li class="youtube"><a href="https://www.youtube.com/rowanuniversity">Rowan on YouTube</a></li> <li class="flickr"><a href="https://www.flickr.com/photos/rowanuniversity">Rowan on Flickr</a></li> </ul> </div> </div> <div class="block block-block" id="block-block-14"> <div class="content"> <div class="footer-global-logo"><img alt="Rowan University logo link to homepage" src="https://www.rowan.edu/_files/_files/images/RowanLogo.png" /></div> <div class="footer-global-address"> <p><span style="white-space: nowrap;">Rowan University</span> • <span style="white-space: nowrap;">201 Mullica Hill Road</span> • <span style="white-space: nowrap;">Glassboro, New Jersey 08028</span> • <span style="white-space: nowrap;">856-256-4000</span></p> </div> </div> </div> <div id="brightedge"> <!-- BrightEdge Autopilot --> <div class="be-ix-link-block"><!--Link Block Target Div--></div> </div> <div class="block block-block" id="block-block-3"> <div class="content"> <p>©2025 Rowan University. <a href="https://sites.rowan.edu/consumer-disclosures/index.html">Consumer Disclosures</a> | <a href="https://catalog.rowan.edu/">University Catalog</a></p> <p>Read the <a href="https://sites.rowan.edu/publicsafety/clery/noticeofavailability.html">Notice of Availability of Rowan’s Annual Security & Fire Safety Report</a></p> </div> </div> </div> </div> </footer> </div> <!-- /#footer /.clearfix --> <script src="https://www.rowan.edu/_files/_files/js/jquery.js" type="text/javascript" ></script> <script src="https://www.rowan.edu/_files/_files/js/jquery-ui.min.js" type="text/javascript" ></script> <script type="text/javascript"> <!--//--><![CDATA[//><!-- window.jQuery || document.write("<script src='/home/sites/all/modules/contrib/jquery_update/replace/jquery/1.8/jquery.js'>\x3C/script>") //--><!]]> </script> <script src="https://www.rowan.edu/_files/_files/js/js__pfiB0OjtfSGm_J2iMbwHpQbdUCT9To1D5U1ABVlK44k__L0A8qWs26Rk87xy2XvJXJxyTdN9x1BcAdqnNPGvC8O8__58f19WGj2bQgjCwoNEZbEWLcxNTlc7jEFer477iHGXk.js" type="text/javascript" ></script> <script defer="defer" src="https://www.rowan.edu/_files/_files/js/js__qw5YOMmR7MBxGcMMNPFP1VyAnTZqd8g0fegdmV9u5VY__cUVy5RMsmKTrg7sKTRBaRlg_Buv9_9YXnpgzRnNRVrc__58f19WGj2bQgjCwoNEZbEWLcxNTlc7jEFer477iHGXk.js" type="text/javascript" ></script> <script src="https://www.rowan.edu/_files/_files/js/js__PS36TmOL4AXbFMuI98uQ068P92PGhbpagpiWKVhIFyc__mQbA2IIgRHDF0uUYH0aQHWPGyxdOKt9T9_g5J3F_YHw__58f19WGj2bQgjCwoNEZbEWLcxNTlc7jEFer477iHGXk.js" type="text/javascript" ></script> <script type="text/javascript"> <!--//--><![CDATA[//><!-- window.CKEDITOR_BASEPATH = '/home/sites/all/libraries/ckeditor/' //--><!]]> </script> <script type="text/javascript"> <!--//--><![CDATA[//><!-- jQuery.extend(Drupal.settings,{"basePath":"\/home\/","pathPrefix":"","ajaxPageState":{"theme":"rowan","theme_token":"z4Ef-1eGutxQ1vbvH3xSy4Ln2m-7t5E5iADKEu2bwdM","css":{"modules\/system\/system.base.css":1,"modules\/system\/system.menus.css":1,"modules\/system\/system.messages.css":1,"modules\/system\/system.theme.css":1,"sites\/all\/modules\/contrib\/calendar\/css\/calendar_multiday.css":1,"modules\/comment\/comment.css":1,"sites\/all\/modules\/contrib\/date\/date_api\/date.css":1,"sites\/all\/modules\/contrib\/date\/date_popup\/themes\/datepicker.1.7.css":1,"sites\/all\/modules\/contrib\/date\/date_repeat_field\/date_repeat_field.css":1,"sites\/all\/modules\/contrib\/domain\/domain_nav\/domain_nav.css":1,"modules\/field\/theme\/field.css":1,"sites\/all\/modules\/contrib\/google_cse\/google_cse.css":1,"modules\/node\/node.css":1,"modules\/search\/search.css":1,"modules\/user\/user.css":1,"sites\/all\/modules\/custom\/uwsbasecamp\/css\/styles.css":1,"sites\/all\/modules\/contrib\/views\/css\/views.css":1,"sites\/all\/modules\/contrib\/ctools\/css\/ctools.css":1,"sites\/all\/modules\/contrib\/isotope\/css\/isotope.css":1,"sites\/all\/modules\/custom\/rowan_stock\/css\/rowan-site.css":1,"sites\/all\/modules\/contrib\/webform\/css\/webform.css":1,"sites\/all\/themes\/oho_basic_responsive\/styles\/normalize.css":1,"sites\/all\/themes\/oho_basic_responsive\/styles\/grid.css":1,"sites\/all\/themes\/oho_basic_responsive\/styles\/globals.css":1,"sites\/all\/themes\/rowan\/styles\/css\/mixins.css":1,"sites\/all\/themes\/rowan\/styles\/css\/global.css":1,"sites\/all\/themes\/rowan\/styles\/css\/typography.css":1,"sites\/all\/themes\/rowan\/styles\/css\/navigation.css":1,"sites\/all\/themes\/rowan\/styles\/css\/home.css":1,"sites\/all\/themes\/rowan\/styles\/css\/rowan-today.css":1,"sites\/all\/themes\/rowan\/styles\/css\/events.css":1,"sites\/all\/themes\/rowan\/styles\/css\/wysiwyg.css":1,"sites\/all\/themes\/rowan\/styles\/css\/flexbox.css":1,"sites\/all\/themes\/rowan\/styles\/css\/full-width.css":1,"sites\/all\/themes\/rowan\/styles\/css\/blogs.css":1,"sites\/all\/themes\/rowan\/styles\/css\/mentorship.css":1,"sites\/all\/themes\/rowan\/styles\/css\/jobs.css":1,"sites\/all\/themes\/rowan\/styles\/css\/publications.css":1,"sites\/all\/themes\/rowan\/styles\/css\/overrides.css":1,"sites\/all\/themes\/rowan\/styles\/css\/colleges.css":1,"sites\/all\/themes\/rowan\/styles\/css\/offices.css":1,"sites\/all\/themes\/rowan\/styles\/css\/maps.css":1,"sites\/all\/themes\/rowan\/styles\/css\/catalogs.css":1,"sites\/all\/themes\/rowan\/styles\/css\/users.css":1,"sites\/all\/themes\/rowan\/styles\/css\/gallery.css":1,"sites\/all\/themes\/rowan\/styles\/css\/doctors.css":1,"sites\/all\/themes\/rowan\/styles\/css\/tourform.css":1,"sites\/all\/themes\/rowan\/styles\/css\/emergency.css":1,"sites\/all\/themes\/rowan\/styles\/fonts\/font-awesome\/font-awesome.css":1,"sites\/all\/themes\/rowan\/styles\/fonts\/proximanova_semibold_macroman\/stylesheet1.css":1,"sites\/all\/themes\/rowan\/styles\/fonts\/proximanova_regular_macroman\/stylesheet2.css":1,"sites\/all\/themes\/rowan\/styles\/fonts\/proximanova_bold_macroman\/stylesheet3.css":1,"sites\/all\/themes\/rowan\/styles\/fonts\/proximanova_black_macroman\/stylesheet4.css":1,"sites\/all\/themes\/rowan\/styles\/css\/print.css":1,"0":1},"js":{"\/\/ajax.googleapis.com\/ajax\/libs\/jquery\/1.8.3\/jquery.js":1,"misc\/jquery.once.js":1,"misc\/drupal.js":1,"sites\/all\/libraries\/isotope\/jquery.isotope.min.js":1,"sites\/all\/modules\/contrib\/google_cse\/google_cse.js":1,"sites\/all\/modules\/custom\/flexbox\/flexbox.js":1,"sites\/all\/modules\/contrib\/floating_block\/floating_block.js":1,"sites\/all\/modules\/custom\/oho_twitter\/js\/customTwitter.js":1,"sites\/all\/modules\/custom\/rowan_rtlm\/js\/rowan-rtlm.js":1,"sites\/all\/modules\/custom\/rowan_stock\/js\/rowan-site.js":1,"sites\/all\/libraries\/form-defaults\/jquery.form-defaults.min.js":1,"sites\/all\/modules\/contrib\/webform_hints\/js\/webform_hints.js":1,"sites\/all\/modules\/contrib\/webform_conditional\/webform_conditional.js":1,"sites\/all\/modules\/contrib\/webform\/js\/webform.js":1,"sites\/all\/modules\/contrib\/google_analytics\/googleanalytics.js":1,"sites\/all\/modules\/contrib\/piwik\/piwik.js":1,"sites\/all\/themes\/rowan\/js\/respond.min.js":1,"sites\/all\/themes\/rowan\/js\/jquery.hoverIntent.js":1,"sites\/all\/themes\/rowan\/js\/equal-col-heights.js":1,"sites\/all\/themes\/rowan\/js\/scripts.js":1,"sites\/all\/themes\/rowan\/js\/home.js":1,"sites\/all\/themes\/rowan\/js\/jquery.cycle2.min.js":1,"sites\/all\/themes\/rowan\/js\/jquery.cycle2.carousel.js":1,"sites\/all\/themes\/rowan\/js\/jquery.cycle2.swipe.min.js":1,"sites\/all\/themes\/rowan\/js\/oho-gallery.js":1,"sites\/all\/modules\/custom\/rowan_emergency\/js\/rowanemergency.jquery.js":1}},"floating_block":{".domain-rowan-today #sidebar-first":{"container":"#main"}},"googleCSE":{"cx":"005402677075098396477:q5jvxusx9xi","language":"","resultsWidth":600,"domain":"www.google.com"},"webform_conditional_webform_client_form_9659":{"fields":false,"nid":"9659","showSpeed":null},"urlIsAjaxTrusted":{"\/home\/academics\/degrees-programs":true,"http:\/\/search.rowan.edu\/search":true},"better_exposed_filters":{"views":{"basic_page":{"displays":{"block_2":{"filters":[]}}},"bottom_blocks":{"displays":{"block_11":{"filters":[]},"block_10":{"filters":[]},"block_5":{"filters":[]},"block_9":{"filters":[]},"block_8":{"filters":[]},"block_13":{"filters":[]},"block_3":{"filters":[]},"block_12":{"filters":[]}}}}},"googleanalytics":{"trackOutbound":1,"trackMailto":1,"trackDownload":1,"trackDownloadExtensions":"7z|aac|arc|arj|asf|asx|avi|bin|csv|doc(x|m)?|dot(x|m)?|exe|flv|gif|gz|gzip|hqx|jar|jpe?g|js|mp(2|3|4|e?g)|mov(ie)?|msi|msp|pdf|phps|png|ppt(x|m)?|pot(x|m)?|pps(x|m)?|ppam|sld(x|m)?|thmx|qtm?|ra(m|r)?|sea|sit|tar|tgz|torrent|txt|wav|wma|wmv|wpd|xls(x|m|b)?|xlt(x|m)|xlam|xml|z|zip","trackDomainMode":"1"},"piwik":{"trackMailto":1}}); //--><!]]> </script> <script src="https://www.rowan.edu/_files/_files/js/emergency.js" type="text/javascript" ></script> <script src="https://www.rowan.edu/_files/_files/js/jquery.flexslider-min.js" ></script> <script src="https://www.rowan.edu/_files/_files/js/moment/moment.min.js" ></script> <script src="https://www.rowan.edu/_files/_files/js/rssfeed.js" ></script> <script src="https://www.rowan.edu/_files/_files/js/scripts.js" ></script> <script src="https://sites.rowan.edu/shared-resources/custom-modules/files/js/custom-modules.js" ></script> <div id="ads" ></div> </body> </html>