Gene & Cell Therapy Education | ASGCT - American Society of Gene & Cell Therapy |

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class="navDropToggle"></div> </li> <li> <a href="/support">Support</a> </li> </ul> <a href="asgct.org" class="px-1 is-external is-hidden-desktop">ASGCT.org</a> </div> </nav> <div class="c-banner" style="background: url('/getattachment/Home/Sickle_Cell_Disease_1280x720_7_00000.png.aspx') 50%/cover no-repeat;"> <div class="c-banner-content container"> <h1>Gene & Cell Therapy Education</h1> <hr /> <p class="is-large">Scientific, reliable information for patients and the public</p> </div> </div> </header> <main class="c-main" id="content"> <section class="section mb-6"> <div class="container"> <div class="c-cta c-cta-primary pt-6"> <div class="c-cta-wrap columns is-vcentered"> <div class="column is-5"> <div class="c-cta-content"> <h2>Empowering Patients 2025: A Cell and Gene Therapies Summit</h2> <p>Join us for a new virtual event providing timely education and engaging discussions on cell and gene therapies with the goal of empowering advocates, patients, and caregivers who are vital in developing treatments.</p> <a href="https://www.asgct.org/asgct-events/march-2025/empowering-patients-2025-a-cell-and-gene-therapie" class="c-button-secondary" target="_self">Learn More + Register</a> </div> </div> <div class="column is-6 is-offset-1 is-centered"> <img src="/getattachment/Home/Gene-Cell-Therapy-101-(1)/GT-1-Illustrations-05-V2.png.aspx" alt="Scientist looking at a DNA strand" /> </div> </div> </div> </div> </section> <section class="section wrap pattern pb-x1" style="background: url('/PatientEducation/media/PatientEducation/square-background.png') repeat;"> <div class="container pt-6"> <div class="columns"> <div class="column is-three-fifths is-offset-one-fifth is-centered"> <h2>Disease Treatments</h2><p>Learn more about how gene therapy works for specific diseases.</p> </div> </div> <div class="columns"> <div class="column is-10 is-offset-1"> <div class="c-tile-wrap mb-5"> <div class="c-tile"> <a href="/disease-treatments/car-t-basics" class="c-tile-link"> <h3>CAR-T Basics</h3> <hr /> <p>Learn about approved treatments for blood cancers, such as leukemia and lymphoma.</p> </a> </div> <div class="c-tile"> <a href="/disease-treatments/gaucher-disease" class="c-tile-link"> <h3>Gaucher Disease</h3> <hr /> <p>Learn about this rare genetic disorder that causes harmful buildup of glycolipids throughout the body and how gene therapy may be able to address its symptoms.</p> </a> </div> <div class="c-tile"> <a href="/disease-treatments/leukodystrophy" class="c-tile-link"> <h3>Leukodystrophies</h3> <hr /> <p>These are a set of rare genetic disorders including cerebral adrenoleukodystrophy (CALD) and metachromatic leukodystrophy (MLD).</p> </a> </div> </div> </div> </div> <div class="columns"> <div class="column is-half is-offset-one-quarter is-centered"> <a href="/disease-treatments" class="c-button-secondary">See All</a> </div> </div> </div> </section> <section class="section wrap blue"> <div class="container"> <div class="c-cta c-cta-secondary"> <div class="c-cta-wrap columns is-vcentered"> <div class="column"> <img src="/getattachment/Home/ASGCT-Clinical-Trials-Finder/TPP-PE-Highlight.png.aspx" alt="One person writing on a clipboard, one person at a computer" /> </div> <div class="column c-cta-content-wrap"> <div class="c-cta-content"> <h2>Subscribe to The Patient Press</h2> <p>Stay up to date on news and events relevant to patients, caregivers, advocates, and anyone else affected by rare diseases. Sign up to get each issue delivered straight to your inbox every other month!</p> <a href="https://asgct.informz.net/asgct/pages/Patient_Press_Signup" class="c-button-secondary is-external" target="_blank">Subscribe</a> </div> </div> </div> </div> </div> </section> <section class="section wrap pattern pb-x1" style="background: url('/PatientEducation/media/PatientEducation/square-background.png') repeat;"> <div class="container pt-6"> <div class="columns"> <div class="column is-three-fifths is-offset-one-fifth is-centered"> <h2>Patient Journey</h2><p>Helpful information to guide you through the challenging journey from diagnosis to pursuing a gene therapy.</p> </div> </div> <div class="columns"> <div class="column is-10 is-offset-1"> <div class="c-tile-wrap mb-5"> <div class="c-tile"> <a href="/patient-journey/identifying-a-genetic-disease" class="c-tile-link"> <h3>Identifying a Genetic Disease</h3> <hr /> <p>Genetic testing, in a variety of forms, is one way to identify rare genetic diseases.</p> </a> </div> <div class="c-tile"> <a href="/patient-journey/next-steps-with-a-diagnosis" class="c-tile-link"> <h3>Next Steps With a Diagnosis</h3> <hr /> <p>Here are information and resources to take some first steps after you've received a confirmed diagnosis of a rare genetic disorder.</p> </a> </div> <div class="c-tile"> <a href="/patient-journey/stimulating-research" class="c-tile-link"> <h3>Stimulating Research</h3> <hr /> <p>Patients and advocates play an important role to initiate gene therapy research.</p> </a> </div> <div class="c-tile"> <a href="/patient-journey/considering-a-clinical-trial" class="c-tile-link"> <h3>Considering a Clinical Trial</h3> <hr /> <p>Here's a glimpse into using the clinical trials finder and what to expect when entering a clinical trial.</p> </a> </div> <div class="c-tile"> <a href="/patient-journey/ethical-issues-germline-gene-editing" class="c-tile-link"> <h3>Ethical Issues: Germline Gene Editing</h3> <hr /> <p>This page addresses key ethical questions that patients, their families, and the public might have about this technology.</p> </a> </div> <div class="c-tile"> <a href="/patient-journey/ethical-issues-illegitimate-clinical-trials" class="c-tile-link"> <h3>Ethical Issues: Unproven Stem Cell Products</h3> <hr /> <p>Learn about some of the signs that might help you decide whether a provider of cell therapies can be trusted.</p> </a> </div> </div> </div> </div> </div> </section> <section class="section mb-6"> <div class="container"> <div class="c-cta c-cta-primary pt-6"> <div class="c-cta-wrap columns is-vcentered"> <div class="column is-5"> <div class="c-cta-content"> <h2>Patient Education Program Wins National Award</h2> <p>We are thrilled to announce that ASGCT has been named a winner of the 2021 "Power of A" Silver Award from the American Society of Association Executives (ASAE) for our Patient Education Program!</p> <a href="https://patienteducation.asgct.org/about-asgct/2021-power-of-a-silver-award" class="c-button-secondary is-external" target="_blank">Learn More</a> </div> </div> <div class="column is-6 is-offset-1 is-centered"> <img src="/getattachment/Home/About-ASGCT/POA-2021-Award-Badges-Silver.png.aspx" alt="power of a award" /> </div> </div> </div> </div> </section> </main> <footer class="c-footer"> <div class="c-footer-primary"> <section class="section"> <div class="container"> <div class="columns"> <div class="column c-footer-section"> <p><img alt="" src="/PatientEducation/media/PatientEducation/logo_white.png" /></p> <p>20800 Swenson Dr., Suite 300<br /> Waukesha, WI 53186</p> </div> <div class="column is-two-fifths c-footer-section"> <ul class="c-utility-list"> <li><a href="#">Gene Therapy 101</a></li> <li><a href="#">Disease Treatments</a></li> <li><a href="#">Clinical Trials</a></li> <li><a href="/patient-journey">Patient Journey</a></li> <li><a href="/about-asgct">About</a></li> <li><a href="/support">Support</a></li> <li><a href="https://asgct.org/about/privacy-policy" target="_blank">Privacy Policy</a></li> </ul> </div> <div class="column c-footer-section"> <h3 class="mb-3">Connect with ASGCT</h3> <p class="mb-0"><span>Phone: 414</span>.278.1341</p> <p><a href="mailto:info@asgct.org">info@asgct.org</a></p> <p> <div class="c-social"> <ul class="c-social-list"> <li class="c-social-item"><a href="https://twitter.com/ASGCTherapy" target="_blank" class="c-social-link twitter"><span class="is-sr-only">Twitter</span></a></li> <li class="c-social-item"><a href="https://www.facebook.com/ASGCTherapy" target="_blank" class="c-social-link facebook"><span class="is-sr-only">Facebook</span></a></li> <li class="c-social-item"><a href="https://www.instagram.com/asgctherapy" target="_blank" class="c-social-link instagram"><span class="is-sr-only">Instagram</span></a></li> <li class="c-social-item"><a href="https://www.linkedin.com/company/asgct" target="_blank" class="c-social-link linkedin"><span 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American Society of Gene & Cell Therapy.</p> <p class="is-tiny">Web design by <a href="https://www.reasononeinc.com/kentico" target="_blank">Reason One</a>. Powered by <a href="http://www.kentico.com" target="_blank">Kentico</a>.</p> </div> </div> </div> </section> </div> </footer> <div class="CookieConsent"> <span id="ctl00_cookieLawQ_lblText" class="ConsentText">This site uses cookies to offer you a better user experience and to analyze site traffic. 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