The importance of the patient voice in the rare disease market l Insights l ICON plc

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This is based on a recognition that, especially in life threatening and rare diseases, there is often an additional perspective that the patient provides on the disease that is not captured by the medical environment. Patients generally participate in the regulatory process as representatives of specific rare disease advocacy organisations providing insight on what their organisation considers are key points about the disease to account for in drug approval, or as an individual patient expert in their therapy area, giving insight on what they, as consumers, feel is most important in the specific treatment for their disease.</p> <p>Study sponsors need to consider the patient perspective in the study design from the earliest stage of study concept and protocol development. This can be done using information from medical literature, qualitative patient interviews, patient questionnaires, and patient workshops.</p> <p>Rare disease patients are most likely to find out about a trial from their treating physician, and typically, rare disease physicians will be in a practice specialising in rare disease treatments and have multiple trial opportunities. Study sponsors need to ensure that physicians at enrolling sites are able to describe the study value to patients and communicate how the trial process has been designed to ensure minimal patient discomfort and lifestyle disruption. Participation by patients requires study sponsors to arrange for travel and lodging, and provide other support services based on a comprehensive assessment of that patient and their family’s individual needs and circumstances.</p> <p>ICON’s experts can help you navigate the clinical development challenges in rare and orphan diseases. To speak with one of our experts, please contact us.</p> <p><em>This blog is an edited version of a media article written by ICON experts William Maier and Kelly Franchetti, “Patient voices in the industry”, which is published in the October 2019 edition of European Biopharmaceutical Review, pages 28-32. © Samedan Ltd.</em></p> </div> <a class="btn btn-primary btn-md" href="https://www2.iconplc.com/Article_EBR_Rare_Diseases" target="_blank">Download Media Article</a> </div> </div> </div> </div> </div> </div> </div> </div> <div id="71f87bc7-a360-4dee-8361-da18c2c72e24"> <div class="bg-gray"> <div class="container-fluid container-fluid--xl text-and-picture-wrapper") }}> <div class="row"> <div class="col-sm"> <div class="text-picture-wrapper"> <div class="text-picture text-picture--text-only text-left with-separator--top"> <div> <div class="text-picture__text"> <h2>Rare and orphan diseases insights</h2> <h3> </h3> <div> <p>ICON's Rare and Orphan Diseases team provides analysis including whitepapers, blogs and contributions to media and industry conversations relating to all aspects of rare and orphan diseases in clinical trials.</p> </div> <a class="btn btn-primary btn-md" href="/insights/therapeutics/rare-and-orphan-diseases" target="_self">Read more </a> </div> </div> </div> </div> </div> </div> </div> </div> </div> </div> </second> </div> <div class="col-md-3 order-1"> <div id="0943c7d4-c0e1-4095-8d43-34b06ebdfed1"> <div class="container-fluid container-fluid--xl sidebar-menu-wrapper"> <div class="sidebar"> <div class="sidebar sidebar--sticky sidebar--collapsible"> <a class="sidebar--collapsible__toggle collapsed" role="button" data-toggle="collapse" href="#sidebar-content" aria-expanded="false" aria-controls="sidebar-content"> <span>In this section</span> </a> <div class="sidebar--collapsible__content collapse" id="sidebar-content"> <div class="sidebar--menu"> <h6 class="d-none d-md-block">In this section</h6> <ul class="sidebar--collapsible__list"> <li 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data-drupal-link-system-path="node/33619">Transforming Medical Device Development with mHealth</a> <div class="collapse " id="remote-patient-monitoring----transforming-medical-device-development-with-mhealth-10604" > </div> </li> </ul> </div> </li> <li> <a href="/insights/digital-disruption/personalising-digital-health" data-drupal-link-system-path="node/33620">Personalising Digital Health</a> <div class="collapse " id="digital-disruption-----------personalising-digital-health-10605" > </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#digital-disruption------------real-world-data-10606"></span> <a href="/insights/digital-disruption/real-world-data" data-drupal-link-system-path="node/33621">Real World Data</a> <div class="collapse " id="digital-disruption------------real-world-data-10606" > <ul class="menu menu-level-2"> <li> <a href="/insights/digital-disruption/real-world-data/maximise-rwe-value" data-drupal-link-system-path="node/33622">Harnessing technology to maximise Real World Evidence value</a> <div class="collapse " id="real-world-data-harnessing-technology-to-maximise-real-world-evidence-value-10607" > </div> </li> <li> <a href="/insights/digital-disruption/real-world-data/meeting-evidentiary-needs" data-drupal-link-system-path="node/33623">Meeting Evidentiary Needs with EHRs</a> <div class="collapse " id="real-world-data--meeting-evidentiary-needs-with-ehrs-10608" > </div> </li> <li> <a href="/insights/digital-disruption/real-world-data/post-market-surveillance" data-drupal-link-system-path="node/33624">Post-Market Surveillance for Medical Devices</a> <div class="collapse " id="real-world-data---post-market-surveillance-for-medical-devices-10609" > </div> </li> </ul> </div> </li> <li> <a href="/insights/digital-disruption/triad-trust-navigating-real-world-healthcare-data-integration" data-drupal-link-system-path="node/40066">The triad of trust: Navigating real-world healthcare data integration</a> <div class="collapse " id="digital-disruption-------------the-triad-of-trust-navigating-real-world-healthcare-data-integration-11271" > </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#patient-centricity-10610"></span> <a href="/insights/patient-centricity" data-drupal-link-system-path="node/33633">Patient Centricity</a> <div class="collapse " id="patient-centricity-10610" > <ul class="menu menu-level-1"> <li> <a href="/insights/patient-centricity/agile-clinical-monitoring" data-drupal-link-system-path="node/33626">Agile Clinical Monitoring</a> <div class="collapse " id="patient-centricity-agile-clinical-monitoring-10611" > </div> </li> <li> <a href="/insights/patient-centricity/capturing-the-voice-of-the-patient-in-clinical-trials" data-drupal-link-system-path="node/33627">Capturing the voice of the patient in clinical trials</a> <div class="collapse " id="patient-centricity--capturing-the-voice-of-the-patient-in-clinical-trials-10612" > </div> </li> <li> <a href="/insights/patient-centricity/charting-the-managed-access-program" data-drupal-link-system-path="node/33628">Charting the Managed Access Program Landscape</a> <div class="collapse " id="patient-centricity---charting-the-managed-access-program-landscape-10613" > </div> </li> <li> <a href="/insights/patient-centricity/developing-nurse-centric-medical-communications" data-drupal-link-system-path="node/33629">Developing Nurse-Centric Medical Communications</a> <div class="collapse " id="patient-centricity----developing-nurse-centric-medical-communications-10614" > </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#patient-centricity-----diversity-and-inclusion-in-clinical-trials-10615"></span> <a href="/insights/patient-centricity/diversity-and-inclusion-clinical-trials" data-drupal-link-system-path="node/33631">Diversity and inclusion in clinical trials</a> <div class="collapse " id="patient-centricity-----diversity-and-inclusion-in-clinical-trials-10615" > <ul class="menu menu-level-2"> <li> <a href="/insights/patient-centricity/diversity-and-inclusion-in-clinical-trials/diversity-and-inclusion-in-clinical-trials-whitepaper" data-drupal-link-system-path="node/33630">Diversity and inclusion in clinical trials whitepaper</a> <div class="collapse " id="diversity-and-inclusion-in-clinical-trials-diversity-and-inclusion-in-clinical-trials-whitepaper-10616" > </div> </li> </ul> </div> </li> <li> <a href="/insights/patient-centricity/exploring-the-patient-perspective-from-different-angles" data-drupal-link-system-path="node/33632">Exploring the patient perspective from different angles</a> <div class="collapse " id="patient-centricity------exploring-the-patient-perspective-from-different-angles-10617" > </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#patient-centricity-------patient-safety-and-pharmacovigilance-10618"></span> <a href="/insights/patient-centricity/patient-safety-and-pharmacovigilance" data-drupal-link-system-path="node/33635">Patient safety and pharmacovigilance</a> <div class="collapse " id="patient-centricity-------patient-safety-and-pharmacovigilance-10618" > <ul class="menu menu-level-2"> <li> <a href="/insights/patient-centricity/patient-safety-and-pharmacovigilance/a-guide-to-safety-data-migrations" data-drupal-link-system-path="node/33634">A guide to safety data migrations</a> <div class="collapse " id="patient-safety-and-pharmacovigilance-a-guide-to-safety-data-migrations-10619" > </div> </li> <li> <a href="/insights/patient-centricity/patient-safety-and-pharmacovigilance/taking-safety-reporting-next-level" data-drupal-link-system-path="node/33636">Taking safety reporting to the next level with automation</a> <div class="collapse " id="patient-safety-and-pharmacovigilance--taking-safety-reporting-to-the-next-level-with-automation-10620" > </div> </li> <li> <a href="/insights/patient-centricity/patient-safety-and-pharmacovigilance/outsourced-pharmacovigilance" data-drupal-link-system-path="node/33637">Outsourced Pharmacovigilance Affiliate Solution</a> <div class="collapse " id="patient-safety-and-pharmacovigilance---outsourced-pharmacovigilance-affiliate-solution-10621" > </div> </li> <li> <a href="/insights/patient-centricity/patient-safety-and-pharmacovigilance/evolution-pharmacovigilance-system" data-drupal-link-system-path="node/33638">The evolution of the Pharmacovigilance System Master File: Benefits, challenges, and opportunities</a> <div class="collapse " id="patient-safety-and-pharmacovigilance----the-evolution-of-the-pharmacovigilance-system-master-file-benefits-challenges-and-opportunities-10622" > </div> </li> <li> <a href="/insights/patient-centricity/patient-safety-and-pharmacovigilance/sponsor-and-cro-pharmacovigilance-and-safety-alliances" data-drupal-link-system-path="node/33639">Sponsor and CRO pharmacovigilance and safety alliances</a> <div class="collapse " id="patient-safety-and-pharmacovigilance-----sponsor-and-cro-pharmacovigilance-and-safety-alliances-10623" > </div> </li> <li> <a href="/insights/patient-centricity/patient-safety-and-pharmacovigilance/understanding-the-periodic-benefit-risk-evaluation-report" data-drupal-link-system-path="node/33640">Understanding the Periodic Benefit-Risk Evaluation Report</a> <div class="collapse " id="patient-safety-and-pharmacovigilance------understanding-the-periodic-benefit-risk-evaluation-report-10624" > </div> </li> </ul> </div> </li> <li> <a href="/insights/patient-centricity/patient-voice-survey" data-drupal-link-system-path="node/33642">Patient voice survey</a> <div class="collapse " id="patient-centricity--------patient-voice-survey-10625" > </div> </li> <li> <a href="/insights/patient-centricity/patient-voice-survey-decentralised-and-hybrid-trials" data-drupal-link-system-path="node/33641">Patient Voice Survey - Decentralised and Hybrid Trials</a> <div class="collapse " id="patient-centricity---------patient-voice-survey-decentralised-and-hybrid-trials-10626" > </div> </li> <li> <a href="/insights/patient-centricity/reimagining-patient-centricity-with-the-iomt" data-drupal-link-system-path="node/33643">Reimagining Patient-Centricity with the Internet of Medical Things (IoMT)</a> <div class="collapse " id="patient-centricity----------reimagining-patient-centricity-with-the-internet-of-medical-things-iomt--10627" > </div> </li> <li> <a href="/insights/patient-centricity/using-longitudinal-qualitative-research-to-capture-the-patient-voice" data-drupal-link-system-path="node/33644">Using longitudinal qualitative research to capture the patient voice</a> <div class="collapse " id="patient-centricity-----------using-longitudinal-qualitative-research-to-capture-the-patient-voice-10628" > </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#regulatory-intelligence-10629"></span> <a href="/insights/regulatory-intelligence" data-drupal-link-system-path="node/33659">Regulatory Intelligence</a> <div class="collapse " id="regulatory-intelligence-10629" > <ul class="menu menu-level-1"> <li> <a href="/insights/regulatory/an-innovative-approach-to-rare-disease-clinical-development" data-drupal-link-system-path="node/33646">An innovative approach to rare disease clinical development</a> <div class="collapse " id="regulatory-intelligence-an-innovative-approach-to-rare-disease-clinical-development-10630" > </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#regulatory-intelligence--eu-clinical-trials-regulation-10631"></span> <a href="/insights/regulatory-intelligence/eu-clinical-trials-regulation" data-drupal-link-system-path="node/33650">EU Clinical Trials Regulation</a> <div class="collapse " id="regulatory-intelligence--eu-clinical-trials-regulation-10631" > <ul class="menu menu-level-2"> <li> <a href="/insights/regulatory/eu-ctr/ema-guideline-on-computerised-systems-and-electronic-data" data-drupal-link-system-path="node/33648">EMA guideline on computerised systems and electronic data in clinical trials</a> <div class="collapse " id="eu-clinical-trials-regulation-ema-guideline-on-computerised-systems-and-electronic-data-in-clinical-trials-10632" > </div> </li> <li> <a href="/insights/regulatory/eu-ctr/eu-clinical-trials-regulation" data-drupal-link-system-path="node/33649">EU CTR Whitepaper</a> <div class="collapse " id="eu-clinical-trials-regulation--eu-ctr-whitepaper-10633" > </div> </li> </ul> </div> </li> <li> <a href="/insights/regulatory-intelligence/accelerate-regulatory-document-writing" data-drupal-link-system-path="node/33645">Using innovative tools and lean writing processes to accelerate regulatory document writing</a> <div class="collapse " id="regulatory-intelligence---using-innovative-tools-and-lean-writing-processes-to-accelerate-regulatory-document-writing-10634" > </div> </li> <li> <a href="/insights/regulatory-intelligence/current-overview-data-sharing-within-clinical-trial-transparency" data-drupal-link-system-path="node/33647">Current overview of data sharing within clinical trial transparency</a> <div class="collapse " id="regulatory-intelligence----current-overview-of-data-sharing-within-clinical-trial-transparency-10635" > </div> </li> <li> <a href="/insights/regulatory/global-agency-meetings" data-drupal-link-system-path="node/33658">Global Agency Meetings: A collaborative approach to drug development</a> <div class="collapse " id="regulatory-intelligence-----global-agency-meetings-a-collaborative-approach-to-drug-development-10643" > </div> </li> <li> <a href="/insights/regulatory-intelligence/keeping-end-mind-key-considerations-creating-plain-language" data-drupal-link-system-path="node/33660">Keeping the end in mind: key considerations for creating plain language summaries</a> <div class="collapse " id="regulatory-intelligence------keeping-the-end-in-mind-key-considerations-for-creating-plain-language-summaries-10644" > </div> </li> <li> <a href="/insights/regulatory-intelligence/navigating-orphan-drug-development-early-phase-marketing" data-drupal-link-system-path="node/33661">Navigating orphan drug development from early phase to marketing authorisation</a> <div class="collapse " id="regulatory-intelligence-------navigating-orphan-drug-development-from-early-phase-to-marketing-authorisation-10645" > </div> </li> <li> <a href="/insights/regulatory-intelligence/procedural-and-regulatory-know-how-china-biotechs-eu" data-drupal-link-system-path="node/33662">Procedural and regulatory know-how for China biotechs in the EU</a> <div class="collapse " id="regulatory-intelligence--------procedural-and-regulatory-know-how-for-china-biotechs-in-the-eu-10646" > </div> </li> <li> <a href="/insights/regulatory/race-act" data-drupal-link-system-path="node/33663">RACE for Children Act</a> <div class="collapse " id="regulatory-intelligence---------race-for-children-act-10647" > </div> </li> <li> <a href="/insights/regulatory/regulatory-considerations-for-biotech" data-drupal-link-system-path="node/33665">Early engagement and regulatory considerations for biotech</a> <div class="collapse " id="regulatory-intelligence----------early-engagement-and-regulatory-considerations-for-biotech-10649" > </div> </li> <li> <a href="/insights/regulatory-intelligence/regulatory-intelligence-newsletter" data-drupal-link-system-path="node/33666">Regulatory Intelligence Newsletter</a> <div class="collapse " id="regulatory-intelligence-----------regulatory-intelligence-newsletter-10650" > </div> </li> <li> <a href="/insights/regulatory-intelligence/requirements-strategy-considerations-within-clinical-trial" data-drupal-link-system-path="node/33667">Requirements & strategy considerations within clinical trial transparency</a> <div class="collapse " id="regulatory-intelligence------------requirements-strategy-considerations-within-clinical-trial-transparency-10651" > </div> </li> <li> <a href="/insights/regulatory/spotlight-on-regulatory-reforms-in-china" data-drupal-link-system-path="node/33668">Spotlight on regulatory reforms in China</a> <div class="collapse " id="regulatory-intelligence-------------spotlight-on-regulatory-reforms-in-china-10652" > </div> </li> <li> <a href="/insights/regulatory-intelligence/demystifying-eu-ctr-mdr-and-ivdr" data-drupal-link-system-path="node/41206">Demystifying EU CTR, MDR and IVDR</a> <div class="collapse " id="regulatory-intelligence--------------demystifying-eu-ctr-mdr-and-ivdr-11541" > </div> </li> <li> <a href="/insights/regulatory-intelligence/transfer-marketing-authorisation" data-drupal-link-system-path="node/33669">Transfer of marketing authorisation</a> <div class="collapse " id="regulatory-intelligence---------------transfer-of-marketing-authorisation-10653" > </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#therapeutics-insights-10654"></span> <a href="/insights/therapeutics" data-drupal-link-system-path="node/33684">Therapeutics insights</a> <div class="collapse " id="therapeutics-insights-10654" > <ul class="menu menu-level-1"> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#therapeutics-insights-endocrine-and-metabolic-disorders-11081"></span> <a href="/insights/therapeutics/endocrine-and-metabolic-disorders" data-drupal-link-system-path="node/39061">Endocrine and Metabolic Disorders</a> <div class="collapse " id="therapeutics-insights-endocrine-and-metabolic-disorders-11081" > <ul class="menu menu-level-2"> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#endocrine-and-metabolic-disorders-obesity-10573"></span> <a href="/insights/therapeutics/endocrine-and-metabolic-disorders/obesity" data-drupal-link-system-path="node/33696">Obesity</a> <div class="collapse " id="endocrine-and-metabolic-disorders-obesity-10573" > <ul class="menu menu-level-3"> <li> <a href="/insights/therapeutics/endocrine-and-metabolic-disorders/obesity/addressing-obesitys-impact" data-drupal-link-system-path="node/33695">Addressing obesity's impact across the disease spectrum</a> <div class="collapse " id="obesity-addressing-obesity-s-impact-across-the-disease-spectrum-10574" > </div> </li> <li> <a href="/insights/therapeutics/endocrine-and-metabolic-disorders/obesity/trends-and-challenges-in-obesity-research" data-drupal-link-system-path="node/33697">Trends and challenges in obesity research and clinical trials</a> <div class="collapse " id="obesity--trends-and-challenges-in-obesity-research-and-clinical-trials-10575" > </div> </li> </ul> </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#therapeutics-insights--cardiovascular-10655"></span> <a href="/insights/therapeutics/cardiovascular" data-drupal-link-system-path="node/33670">Cardiovascular</a> <div class="collapse " id="therapeutics-insights--cardiovascular-10655" > <ul class="menu menu-level-2"> <li> <a href="/insights/therapeutics/cardiovascular/mitigating-the-impact-of-covid19-on-cardiovascular-trials" data-drupal-link-system-path="node/33671">Mitigating the impact of COVID-19 on cardiovascular trials</a> <div class="collapse " id="cardiovascular-mitigating-the-impact-of-covid-19-on-cardiovascular-trials-10656" > </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#therapeutics-insights---cell-and-gene-therapies-10657"></span> <a href="/insights/therapeutics/cell-and-gene-therapies" data-drupal-link-system-path="node/33674">Cell and Gene Therapies</a> <div class="collapse " id="therapeutics-insights---cell-and-gene-therapies-10657" > <ul class="menu menu-level-2"> <li> <a href="/insights/therapeutics/cell-and-gene-therapies/approaching-the-car-t-cell-therapy-horizon" data-drupal-link-system-path="node/33672">Approaching the CAR T-cell therapy horizon</a> <div class="collapse " id="cell-and-gene-therapies-approaching-the-car-t-cell-therapy-horizon-10658" > </div> </li> <li> <a href="/insights/therapeutics/cell-and-gene-therapies/cell-and-gene-therapy-clinical-trials" data-drupal-link-system-path="node/33673">Cell and Gene ebook</a> <div class="collapse " id="cell-and-gene-therapies--cell-and-gene-ebook-10659" > </div> </li> <li> <a href="/insights/therapeutics/cell-and-gene-therapies/long-term-follow-up-studies-of-cell-and-gene-therapies" data-drupal-link-system-path="node/33675">Long-term follow-up studies of cell and gene therapies</a> <div class="collapse " id="cell-and-gene-therapies---long-term-follow-up-studies-of-cell-and-gene-therapies-10660" > </div> </li> <li> <a href="/insights/therapeutics/cell-and-gene-therapies/mainstreaming-cell-gene-therapies" data-drupal-link-system-path="node/33676">Mainstreaming Cell & Gene Therapies</a> <div class="collapse " id="cell-and-gene-therapies----mainstreaming-cell-gene-therapies-10661" > </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#therapeutics-insights----central-nervous-system-10662"></span> <a href="/insights/therapeutics/central-nervous-system" data-drupal-link-system-path="node/33679">Central Nervous System</a> <div class="collapse " id="therapeutics-insights----central-nervous-system-10662" > <ul class="menu menu-level-2"> <li> <a href="/insights/therapeutics/central-nervous-system/a-mind-for-digital-therapeutics" data-drupal-link-system-path="node/33677">A mind for digital therapeutics</a> <div class="collapse " id="central-nervous-system-a-mind-for-digital-therapeutics-10663" > </div> </li> <li> <a href="/insights/therapeutics/central-nervous-system/challenges-and-opportunities-in-traumatic-brain-injury-clinical-trials" data-drupal-link-system-path="node/33678">Challenges and opportunities in traumatic brain injury clinical trials</a> <div class="collapse " id="central-nervous-system--challenges-and-opportunities-in-traumatic-brain-injury-clinical-trials-10664" > </div> </li> <li> <a href="/insights/therapeutics/central-nervous-system/key-considerations-for-parkinsons-disease-trials" data-drupal-link-system-path="node/33680">Challenges and opportunities in Parkinson’s Disease clinical trials</a> <div class="collapse " id="central-nervous-system---challenges-and-opportunities-in-parkinson-s-disease-clinical-trials-10665" > </div> </li> <li> <a href="/insights/therapeutics/central-nervous-system/key-considerations-in-chronic-pain-clinical-trials" data-drupal-link-system-path="node/33681">Key Considerations in Chronic Pain Clinical Trials</a> <div class="collapse " id="central-nervous-system----key-considerations-in-chronic-pain-clinical-trials-10666" > </div> </li> </ul> </div> </li> <li> <a href="/insights/therapeutics/glycomics" data-drupal-link-system-path="node/33683">Glycomics</a> <div class="collapse " id="therapeutics-insights-----glycomics-10668" > </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#therapeutics-insights------infectious-diseases-10669"></span> <a href="/insights/therapeutics/infectious-diseases" data-drupal-link-system-path="node/33690">Infectious Diseases</a> <div class="collapse " id="therapeutics-insights------infectious-diseases-10669" > <ul class="menu menu-level-2"> <li> <a href="/insights/therapeutics/infectious-diseases/antimicrobial-resistance" data-drupal-link-system-path="node/33685">Antimicrobial Resistance</a> <div class="collapse " id="infectious-diseases-antimicrobial-resistance-10670" > </div> </li> <li> <a href="/therapeutics/therapeutics-insights/infectious-diseases/considerations-strengthening-vaccine" data-drupal-link-system-path="node/33686">Considerations for strengthening vaccine development</a> <div class="collapse " id="infectious-diseases--considerations-for-strengthening-vaccine-development-10671" > </div> </li> <li> <a href="/insights/therapeutics/infectious-diseases/covid-19-vaccine-trials" data-drupal-link-system-path="node/33687">COVID-19 vaccine trials</a> <div class="collapse " id="infectious-diseases---covid-19-vaccine-trials-10672" > </div> </li> <li> <a href="/insights/therapeutics/infectious-diseases/covid-19-vaccines-pass" data-drupal-link-system-path="node/33688">COVID-19 vaccines: Post-authorisation safety surveillance</a> <div class="collapse " id="infectious-diseases----covid-19-vaccines-post-authorisation-safety-surveillance-10673" > </div> </li> <li> <a href="/insights/therapeutics/infectious-diseases/hiv" data-drupal-link-system-path="node/33689">HIV</a> <div class="collapse " id="infectious-diseases-----hiv-10674" > </div> </li> <li> <a href="/insights/therapeutics/infectious-diseases/the-value-of-dynamic-transmission-models" data-drupal-link-system-path="node/33691">The value of dynamic transmission models</a> <div class="collapse " id="infectious-diseases------the-value-of-dynamic-transmission-models-10675" > </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#therapeutics-insights-------nash-10677"></span> <a href="/insights/therapeutics/nash" data-drupal-link-system-path="node/33693">NASH</a> <div class="collapse " id="therapeutics-insights-------nash-10677" > <ul class="menu menu-level-2"> <li> <a href="/insights/therapeutics/nash/the-voice-of-nash-investigators-in-patient-recruitment" data-drupal-link-system-path="node/33694">The voice of NASH investigators</a> <div class="collapse " id="nash-the-voice-of-nash-investigators-10678" > </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#therapeutics-insights--------oncology-10682"></span> <a href="/insights/therapeutics/oncology" data-drupal-link-system-path="node/33698">Oncology</a> <div class="collapse " id="therapeutics-insights--------oncology-10682" > <ul class="menu menu-level-2"> <li> <a href="/insights/therapeutics/oncology/icon-survey-report-innovation-oncology" data-drupal-link-system-path="node/40826">ICON survey report: Innovation in Oncology</a> <div class="collapse " id="oncology-icon-survey-report-innovation-in-oncology-11406" > </div> </li> <li> <a href="/insights/therapeutics/oncology/de-risking-clinical-development-precision-medicines" data-drupal-link-system-path="node/40831">De-risking clinical development of precision medicines in oncology</a> <div class="collapse " id="oncology--de-risking-clinical-development-of-precision-medicines-in-oncology-11411" > </div> </li> <li> <a href="/insights/therapeutics/oncology/advances-imaging-biomarkers-estimating-drug-efficacy-tumour" data-drupal-link-system-path="node/41156">Advances in imaging biomarkers: Estimating drug efficacy with tumour growth rate modelling</a> <div class="collapse " id="oncology---advances-in-imaging-biomarkers-estimating-drug-efficacy-with-tumour-growth-rate-modelling-11536" > </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#therapeutics-insights---------paediatrics-10683"></span> <a href="/insights/therapeutics/pediatrics" data-drupal-link-system-path="node/33699">Paediatrics</a> <div class="collapse " id="therapeutics-insights---------paediatrics-10683" > <ul class="menu menu-level-2"> <li> <a href="/insights/therapeutics/pediatrics/pediatric-risk-assessment-map" data-drupal-link-system-path="node/33700">Paediatric Risk Assessment Map</a> <div class="collapse " id="paediatrics-paediatric-risk-assessment-map-10684" > </div> </li> </ul> </div> </li> <li> <a href="/insights/therapeutics/respiratory" data-drupal-link-system-path="node/40721">Respiratory</a> <div class="collapse " id="therapeutics-insights----------respiratory-11351" > </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#therapeutics-insights-----------rare-and-orphan-diseases-10685"></span> <a href="/insights/therapeutics/rare-and-orphan-diseases" data-drupal-link-system-path="node/33706">Rare and orphan diseases</a> <div class="collapse " id="therapeutics-insights-----------rare-and-orphan-diseases-10685" > <ul class="menu menu-level-2"> <li> <a href="/insights/therapeutics/rare-and-orphan-diseases/advanced-therapies-for-rare-diseases" data-drupal-link-system-path="node/33701">Advanced therapies for rare diseases</a> <div class="collapse " id="rare-and-orphan-diseases-advanced-therapies-for-rare-diseases-10686" > </div> </li> <li> <a href="/insights/therapeutics/rare-and-orphan-diseases/cross-border-enrollment-of-rare-disease-patients" data-drupal-link-system-path="node/33702">Cross-border enrollment of rare disease patients</a> <div class="collapse " id="rare-and-orphan-diseases--cross-border-enrollment-of-rare-disease-patients-10687" > </div> </li> <li> <a href="/insights/therapeutics/rare-and-orphan-diseases/crossing-the-finish-line" data-drupal-link-system-path="node/33703">Crossing the finish line: Why effective participation support strategy is critical to trial efficiency and success in rare diseases</a> <div class="collapse " id="rare-and-orphan-diseases---crossing-the-finish-line-why-effective-participation-support-strategy-is-critical-to-trial-efficiency-and-success-in-rare-diseases-10688" > </div> </li> <li> <a href="/insights/therapeutics/rare-and-orphan-diseases/diversity-equity-and-inclusion-in-rare-disease-trials" data-drupal-link-system-path="node/33704">Diversity, equity and inclusion in rare disease clinical trials</a> <div class="collapse " id="rare-and-orphan-diseases----diversity-equity-and-inclusion-in-rare-disease-clinical-trials-10689" > </div> </li> <li> <a href="/insights/therapeutics/rare-and-orphan-diseases/identify-and-mitigate-risks-to-rare-disease-clinical-programmes" data-drupal-link-system-path="node/33705">Identify and mitigate risks to rare disease clinical programmes</a> <div class="collapse " id="rare-and-orphan-diseases-----identify-and-mitigate-risks-to-rare-disease-clinical-programmes-10690" > </div> </li> <li> <a href="/insights/therapeutics/rare-and-orphan-diseases/leveraging-historical-data-for-use-in-rare-disease-trials" data-drupal-link-system-path="node/33707">Leveraging historical data for use in rare disease trials</a> <div class="collapse " id="rare-and-orphan-diseases------leveraging-historical-data-for-use-in-rare-disease-trials-10691" > </div> </li> <li> <a href="/insights/therapeutics/rare-and-orphan-diseases/natural-history-studies-to-improve-drug-development-in-rare-diseases" data-drupal-link-system-path="node/33708">Natural history studies to improve drug development in rare diseases</a> <div class="collapse " id="rare-and-orphan-diseases-------natural-history-studies-to-improve-drug-development-in-rare-diseases-10692" > </div> </li> <li> <a href="/insights/therapeutics/rare-and-orphan-diseases/patient-centricity-in-orphan-drug-development" data-drupal-link-system-path="node/33709">Patient Centricity in Orphan Drug Development</a> <div class="collapse " id="rare-and-orphan-diseases--------patient-centricity-in-orphan-drug-development-10693" > </div> </li> <li> <a href="/insights/therapeutics/rare-and-orphan-diseases/the-key-to-remarkable-rare-disease-registries" data-drupal-link-system-path="node/33710">The key to remarkable rare disease registries</a> <div class="collapse " id="rare-and-orphan-diseases---------the-key-to-remarkable-rare-disease-registries-10694" > </div> </li> <li> <a href="/insights/therapeutics/rare-and-orphan-diseases/therapeutic-spotlight-precision-medicine" data-drupal-link-system-path="node/40986">Therapeutic spotlight: Precision medicine considerations in rare diseases</a> <div class="collapse " id="rare-and-orphan-diseases----------therapeutic-spotlight-precision-medicine-considerations-in-rare-diseases-11466" > </div> </li> </ul> </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#transforming-trials-10695"></span> <a href="/insights/transforming-trials" data-drupal-link-system-path="node/33729">Transforming Trials</a> <div class="collapse " id="transforming-trials-10695" > <ul class="menu menu-level-1"> <li> <a href="/insights/transforming-trials/accelerating-biotech-innovation" data-drupal-link-system-path="node/34264">Accelerating biotech innovation from discovery to commercialisation</a> <div class="collapse " id="transforming-trials-accelerating-biotech-innovation-from-discovery-to-commercialisation-10901" > </div> </li> <li> <a href="/insights/transforming-trials/ensuring-validity-clinical-outcomes-assessment-coa-data-value-rater" data-drupal-link-system-path="node/39731">Ensuring the validity of clinical outcomes assessment (COA) data: The value of rater training</a> <div class="collapse " id="transforming-trials--ensuring-the-validity-of-clinical-outcomes-assessment-coa-data-the-value-of-rater-training-11231" > </div> </li> <li> <a href="/insights/transforming-trials/linguistic-validation-of-clinical-outcomes-assessments" data-drupal-link-system-path="node/34286">Linguistic validation of Clinical Outcomes Assessments</a> <div class="collapse " id="transforming-trials---linguistic-validation-of-clinical-outcomes-assessments-10851" > </div> </li> <li> <a href="/insights/transforming-trials/optimising-biotech-funding" data-drupal-link-system-path="node/39001">Optimising biotech funding</a> <div class="collapse " id="transforming-trials----optimising-biotech-funding-11026" > </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#transforming-trials-----adaptive-clinical-trials-10696"></span> <a href="/insights/transforming-trials/adaptive-clinical-trials" data-drupal-link-system-path="node/33712">Adaptive clinical trials</a> <div class="collapse " id="transforming-trials-----adaptive-clinical-trials-10696" > <ul class="menu menu-level-2"> <li> <a href="/insights/transforming-trials/adaptive-clinical-trials/faster-path-to-market" data-drupal-link-system-path="node/33711">Adaptive Design: The Faster Path to Market</a> <div class="collapse " id="adaptive-clinical-trials-adaptive-design-the-faster-path-to-market-10697" > </div> </li> </ul> </div> </li> <li> <a href="/insights/transforming-trials/best-practices-to-increase-engagement-with-medical-and-scientific-poster-content" data-drupal-link-system-path="node/33713">Best practices to increase engagement with medical and scientific poster content</a> <div class="collapse " id="transforming-trials------best-practices-to-increase-engagement-with-medical-and-scientific-poster-content-10698" > </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#transforming-trials-------decentralised-clinical-trials-10701"></span> <a href="/insights/transforming-trials/decentralised-and-hybrid-clinical-trials" data-drupal-link-system-path="node/33718">Decentralised clinical trials</a> <div class="collapse " id="transforming-trials-------decentralised-clinical-trials-10701" > <ul class="menu menu-level-2"> <li> <a href="/insights/transforming-trials/decentralised-and-hybrid-clinical-trials/biopharma-perspective-panel-discussion" data-drupal-link-system-path="node/33716">Biopharma perspective: the promise of decentralised models and diversity in clinical trials</a> <div class="collapse " id="decentralised-clinical-trials-biopharma-perspective-the-promise-of-decentralised-models-and-diversity-in-clinical-trials-10702" > </div> </li> <li> <a href="/insights/transforming-trials/decentralised-and-hybrid-clinical-trials/decentralised-trials-plan" data-drupal-link-system-path="node/33717">Decentralised and Hybrid clinical trials</a> <div class="collapse " id="decentralised-clinical-trials--decentralised-and-hybrid-clinical-trials-10703" > </div> </li> <li> <a href="/insights/transforming-trials/decentralised-and-hybrid-clinical-trials/practical-considerations-in-transitioning-to-dct" data-drupal-link-system-path="node/33719">Practical considerations in transitioning to hybrid or decentralised clinical trials</a> <div class="collapse " id="decentralised-clinical-trials---practical-considerations-in-transitioning-to-hybrid-or-decentralised-clinical-trials-10704" > </div> </li> <li> <a href="/insights/transforming-trials/decentralised-and-hybrid-clinical-trials/regulatory-labyrinth-of-technology" data-drupal-link-system-path="node/33720">Navigating the regulatory labyrinth of technology in decentralised clinical trials</a> <div class="collapse " id="decentralised-clinical-trials----navigating-the-regulatory-labyrinth-of-technology-in-decentralised-clinical-trials-10705" > </div> </li> </ul> </div> </li> <li> <a href="/insights/transforming-trials/ecoa-implementation" data-drupal-link-system-path="node/33721">eCOA implementation</a> <div class="collapse " id="transforming-trials--------ecoa-implementation-10706" > </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#transforming-trials---------blended-solutions-insights-10707"></span> <a href="/insights/transforming-trials/blended-solutions-insights" data-drupal-link-system-path="node/33723">Blended solutions insights</a> <div class="collapse " id="transforming-trials---------blended-solutions-insights-10707" > <ul class="menu menu-level-2"> <li> <a href="/insights/transforming-trials/functional-model-insights/clinical-trials-in-japan-an-enterprise-growth-and-management-strategy" data-drupal-link-system-path="node/33722">Clinical trials in Japan: An enterprise growth and management strategy</a> <div class="collapse " id="blended-solutions-insights-clinical-trials-in-japan-an-enterprise-growth-and-management-strategy-10708" > </div> </li> <li> <a href="/insights/transforming-trials/functional-model-insights/investments-in-supply-of-cras" data-drupal-link-system-path="node/33724">How investments in supply of CRAs is better than competing with the demand for CRAs</a> <div class="collapse " id="blended-solutions-insights--how-investments-in-supply-of-cras-is-better-than-competing-with-the-demand-for-cras-10709" > </div> </li> <li> <a href="/insights/transforming-trials/functional-model-insights/the-evolution-of-fsp-not-just-for-large-pharma" data-drupal-link-system-path="node/33725">The evolution of FSP: not just for large pharma</a> <div class="collapse " id="blended-solutions-insights---the-evolution-of-fsp-not-just-for-large-pharma-10710" > </div> </li> <li> <a href="/insights/transforming-trials/blended-solutions-insights/embracing-blended-operating-model" data-drupal-link-system-path="node/41091">Embracing a blended operating model</a> <div class="collapse " id="blended-solutions-insights----embracing-a-blended-operating-model-11476" > </div> </li> </ul> </div> </li> <li> <a href="/insights/transforming-trials/implications-of-covid-19-on-statistical-design" data-drupal-link-system-path="node/33726">Implications of COVID-19 on statistical design and analyses of clinical studies</a> <div class="collapse " id="transforming-trials----------implications-of-covid-19-on-statistical-design-and-analyses-of-clinical-studies-10711" > </div> </li> <li> <a href="/insights/transforming-trials/improving-pharma-research-and-development-efficiency" data-drupal-link-system-path="node/33727">Improving pharma R&D efficiency</a> <div class="collapse " id="transforming-trials-----------improving-pharma-r-d-efficiency-10712" > </div> </li> <li> <a href="/insights/transforming-trials/increasing-complexity-and-declining-roi-in-drug-development" data-drupal-link-system-path="node/33728">Increasing Complexity and Declining ROI in Drug Development</a> <div class="collapse " id="transforming-trials------------increasing-complexity-and-declining-roi-in-drug-development-10713" > </div> </li> <li> <a href="/insights/transforming-trials/innovation-in-clinical-trial-methodologies" data-drupal-link-system-path="node/33730">Innovation in Clinical Trial Methodologies</a> <div class="collapse " id="transforming-trials-------------innovation-in-clinical-trial-methodologies-10714" > </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#transforming-trials--------------partnership-insights-10715"></span> <a href="/insights/transforming-trials/partnership-insights" data-drupal-link-system-path="node/33732">Partnership insights</a> <div class="collapse " id="transforming-trials--------------partnership-insights-10715" > <ul class="menu menu-level-2"> <li> <a href="/insights/transforming-trials/partnership-insights/exploring-partnership-culture" data-drupal-link-system-path="node/33731">Exploring partnership culture and its impact on outsourcing and operational strategy</a> <div class="collapse " id="partnership-insights-exploring-partnership-culture-and-its-impact-on-outsourcing-and-operational-strategy-10716" > </div> </li> </ul> </div> </li> <li> <a href="/insights/transforming-trials/risk-based-quality-management" data-drupal-link-system-path="node/33733">Risk Based Quality Management</a> <div class="collapse " id="transforming-trials---------------risk-based-quality-management-10717" > </div> </li> <li> <a href="/insights/transforming-trials/transforming-the-rd-model" data-drupal-link-system-path="node/33735">Transforming the R&D Model to Sustain Growth</a> <div class="collapse " id="transforming-trials----------------transforming-the-r-d-model-to-sustain-growth-10719" > </div> </li> </ul> </div> </li> <li class="sidebar--submenu"> <span aria-controls="sidebar-content" class="collapsed " data-toggle="collapse" role="button" href="#value-based-healthcare-10720"></span> <a href="/insights/value-based-healthcare" data-drupal-link-system-path="node/33746">Value Based Healthcare</a> <div class="collapse " id="value-based-healthcare-10720" > <ul class="menu menu-level-1"> <li> <a href="/insights/value-based-healthcare/strategies-commercialising-oncology-treatments-young-adults" data-drupal-link-system-path="node/40021">Strategies for commercialising oncology treatments for young adults</a> <div class="collapse " id="value-based-healthcare-strategies-for-commercialising-oncology-treatments-for-young-adults-11276" > </div> </li> <li> <a href="/insights/value-based-healthcare/US-payers-and-PROs" data-drupal-link-system-path="node/33758">US payers and PROs</a> <div class="collapse " id="value-based-healthcare--us-payers-and-pros-10721" > </div> </li> <li> <a href="/insights/value-based-healthcare/accelerated-early-clinical-manufacturing" data-drupal-link-system-path="node/33736">Accelerated early clinical manufacturing</a> <div class="collapse " id="value-based-healthcare---accelerated-early-clinical-manufacturing-10722" > </div> </li> <li> <a href="/insights/value-based-healthcare/cardiovascular-medical-devices" data-drupal-link-system-path="node/33737">Cardiovascular Medical Devices</a> <div class="collapse " id="value-based-healthcare----cardiovascular-medical-devices-10723" > </div> </li> <li> <a href="/insights/value-based-healthcare/cms-price-negotiation-for-part-d-drugs" data-drupal-link-system-path="node/33738">CMS Part D Price Negotiations: Is your drug on the list?</a> <div class="collapse " id="value-based-healthcare-----cms-part-d-price-negotiations-is-your-drug-on-the-list--10724" > </div> </li> <li> <a href="/insights/value-based-healthcare/covid-19-navigating-global-market-access" data-drupal-link-system-path="node/33739">COVID-19 navigating global market access</a> <div class="collapse " id="value-based-healthcare------covid-19-navigating-global-market-access-10725" > </div> </li> <li> <a href="/insights/value-based-healthcare/ensuring-scientific-rigor-in-external-control-arms" data-drupal-link-system-path="node/33740">Ensuring scientific rigor in external control arms</a> <div class="collapse " id="value-based-healthcare-------ensuring-scientific-rigor-in-external-control-arms-10726" > </div> </li> <li> <a href="/insights/value-based-healthcare/evidence-synthesis" data-drupal-link-system-path="node/33741">Evidence Synthesis: A solution to sparse evidence, heterogeneous studies, and disconnected networks</a> <div class="collapse " id="value-based-healthcare--------evidence-synthesis-a-solution-to-sparse-evidence-heterogeneous-studies-and-disconnected-networks-10727" > </div> </li> <li> <a href="/insights/value-based-healthcare/global-outcomes-benchmark" data-drupal-link-system-path="node/33742">Global Outcomes Benchmarking</a> <div class="collapse " id="value-based-healthcare---------global-outcomes-benchmarking-10728" > </div> </li> <li> <a href="/insights/value-based-healthcare/health-technology-assessm" data-drupal-link-system-path="node/33743">Health technology assessment</a> <div class="collapse " id="value-based-healthcare----------health-technology-assessment-10729" > </div> </li> <li> <a href="/insights/value-based-healthcare/icer" data-drupal-link-system-path="node/33744">Perspectives from US payers</a> <div class="collapse " id="value-based-healthcare-----------perspectives-from-us-payers-10730" > </div> </li> <li> <a href="/insights/value-based-healthcare/icers-impact-on-payer-decision-making" data-drupal-link-system-path="node/33745">ICER’s impact on payer decision making</a> <div class="collapse " id="value-based-healthcare------------icer-s-impact-on-payer-decision-making-10731" > </div> </li> <li> <a href="/insights/value-based-healthcare/making-sense-of-the-biosimilar-market" data-drupal-link-system-path="node/33747">Making Sense of the Biosimilars Market</a> <div class="collapse " id="value-based-healthcare-------------making-sense-of-the-biosimilars-market-10732" > </div> </li> <li> <a href="/insights/value-based-healthcare/medical-communications-in-early-phase-product-development" data-drupal-link-system-path="node/33748">Medical communications in early phase product development</a> <div class="collapse " id="value-based-healthcare--------------medical-communications-in-early-phase-product-development-10733" > </div> </li> <li> <a href="/insights/value-based-healthcare/navigating-challenges-and-opportunities-value-based-healthcare" data-drupal-link-system-path="node/33749">Navigating the Challenges and Opportunities of Value Based Healthcare</a> <div class="collapse " id="value-based-healthcare---------------navigating-the-challenges-and-opportunities-of-value-based-healthcare-10734" > </div> </li> <li> <a href="/insights/value-based-healthcare/payer-reliance-on-icer-assessments-and-perceptions-on-value-based-pricing" data-drupal-link-system-path="node/33750">Payer Reliance on ICER and Perceptions on Value Based Pricing</a> <div class="collapse " id="value-based-healthcare----------------payer-reliance-on-icer-and-perceptions-on-value-based-pricing-10735" > </div> </li> <li> <a href="/insights/value-based-healthcare/payers-perspectives-on-digital-therapeutics" data-drupal-link-system-path="node/33751">Payers Perspectives on Digital Therapeutics</a> <div class="collapse " id="value-based-healthcare-----------------payers-perspectives-on-digital-therapeutics-10736" > </div> </li> <li> <a href="/insights/value-based-healthcare/precision-medicine" data-drupal-link-system-path="node/33752">Precision Medicine</a> <div class="collapse " id="value-based-healthcare------------------precision-medicine-10737" > </div> </li> <li> <a href="/insights/value-based-healthcare/rwe-generation-cross-sect" data-drupal-link-system-path="node/33753">RWE Generation Cross Sectional Studies and Medical Chart Review</a> <div class="collapse " id="value-based-healthcare-------------------rwe-generation-cross-sectional-studies-and-medical-chart-review-10738" > </div> </li> <li> <a href="/insights/value-based-healthcare/survey-results-how-to-engage-healthcare-decision-makers" data-drupal-link-system-path="node/33754">Survey results: How to engage healthcare decision-makers</a> <div class="collapse " id="value-based-healthcare--------------------survey-results-how-to-engage-healthcare-decision-makers-10739" > </div> </li> <li> <a href="/insights/value-based-healthcare/the-affordability-hurdle-for-gene-therapies" data-drupal-link-system-path="node/33755">The affordability hurdle for gene therapies</a> <div class="collapse " id="value-based-healthcare---------------------the-affordability-hurdle-for-gene-therapies-10740" > </div> </li> <li> <a href="/insights/value-based-healthcare/the-role-of-icer-as-an-independent-hta-organisation" data-drupal-link-system-path="node/33756">The Role of ICER as an HTA Organisation</a> <div 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The importance of the patient voice in the rare disease market l Insights l ICON plc