CINXE.COM
Patient Journey | ASGCT - American Society of Gene & Cell Therapy |
<!DOCTYPE html> <html xmlns="http://www.w3.org/1999/xhtml"> <head> <!-- Google Tag Manager --> <script type="text/javascript">(function (w, d, s, l, i) { w[l] = w[l] || []; w[l].push({ 'gtm.start': new Date().getTime(), event: 'gtm.js' }); var f = d.getElementsByTagName(s)[0], j = d.createElement(s), dl = l != 'dataLayer' ? '&l=' + l : ''; j.async = true; j.src = 'https://www.googletagmanager.com/gtm.js?id=' + i + dl; f.parentNode.insertBefore(j, f); })(window, document, 'script', 'dataLayer', 'GTM-NFW5DS9');</script> <!-- End Google Tag Manager --> <!-- Begin Informz Tracking --> <script type="text/javascript"> //------------------------------------------------------- var z_account = "2632C1D8-6432-4D3A-93D6-08AAECC53F86"; var z_collector = "asgct.informz.net"; var z_cookieDomain = ".asgct.org"; //------------------------------------------------------- (function (e, o, n, r, t, a, s) { e[t] || (e.GlobalSnowplowNamespace = e.GlobalSnowplowNamespace || [], e.GlobalSnowplowNamespace.push(t), e[t] = function () { (e[t].q = e[t].q || []).push(arguments) }, e[t].q = e[t].q || [], a = o.createElement(n), s = o.getElementsByTagName(n)[0], a.async = 1, a.src = r, s.parentNode.insertBefore(a, s)) }(window, document, "script", "https://cdn.informz.net/web_trk/sp.js", "informz_trk")), informz_trk("newTracker", "infz", z_collector + "/web_trk/collector/", { appId: z_account, cookieDomain: z_cookieDomain }), informz_trk("setUserIdFromLocation", "_zs"), informz_trk("enableActivityTracking", 30, 15); informz_trk("trackPageView", null); </script> <!-- End Informz Tracking --> <meta charset="utf-8" /> <meta http-equiv="X-UA-Compatible" content="IE=edge" /> <meta name="viewport" content="width=device-width,user-scalable=no,maximum-scale=1.0,initial-scale=1.0" /> <link href="/BlueKey/pe_assets/build/styles.css" rel="stylesheet" /> <script type="text/javascript" defer="defer" src="https://extend.vimeocdn.com/ga/127349852.js"></script> <meta name="twitter:card" content="summary_large_image" /> <meta name="twitter:site" content="https://twitter.com/ASGCTherapy" <meta name="twitter:creator" content="@ASGCTherapy" <meta name="twitter:image" content="~/attachment.aspx" <meta name="description" content="Helpful information to guide you through the challenging journey from diagnosis to pursuing a gene therapy." /> <meta charset="UTF-8" /> <link href="/App_Themes/Default/Images/favicon.ico" type="image/x-icon" rel="shortcut icon" /> <link href="/App_Themes/Default/Images/favicon.ico" type="image/x-icon" rel="icon" /> <title> Patient Journey | ASGCT - American Society of Gene & Cell Therapy | </title></head> <body class="LTR IE IE7 ENUS ContentBody"> <!-- Google Tag Manager (noscript) --> <noscript><iframe src="https://www.googletagmanager.com/ns.html?id=GTM-NFW5DS9" height="0" width="0" style="display:none;visibility:hidden"></iframe></noscript> <!-- End Google Tag Manager (noscript) --> <form method="post" action="/patient-journey/gene-therapy-centers" id="aspnetForm"> <div class="aspNetHidden"> <input type="hidden" name="__CMSCsrfToken" id="__CMSCsrfToken" value="SWPEHNmQ7LtU7tvS3/5VpVsxUYCWvMiP3RezmXtq76IBv9yvvqmFb4vAgyLYWD8/4nLZm759ioK7k04WCIEJoUhGTe4=" /> <input type="hidden" name="__EVENTTARGET" id="__EVENTTARGET" value="" /> <input type="hidden" name="__EVENTARGUMENT" id="__EVENTARGUMENT" value="" /> <input type="hidden" name="__VIEWSTATE" id="__VIEWSTATE" value="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" /> </div> <script type="text/javascript"> //<![CDATA[ var theForm = document.forms['aspnetForm']; if (!theForm) { theForm = document.aspnetForm; } function __doPostBack(eventTarget, eventArgument) { if (!theForm.onsubmit || (theForm.onsubmit() != false)) { theForm.__EVENTTARGET.value = eventTarget; theForm.__EVENTARGUMENT.value = eventArgument; theForm.submit(); } } //]]> </script> <script src="/WebResource.axd?d=UZQNzmZXG1IdUaHxtavOjRvGEvOmz1kvw97PqEaxzBy7Ys-tUotw-RqgdbsvC3g_7cXjehqAdA_N6kbuK73WBAVGdxo1&t=638562384440000000" type="text/javascript"></script> <input type="hidden" name="lng" id="lng" value="en-US" /> <script type="text/javascript"> //<![CDATA[ function PM_Postback(param) { if (window.top.HideScreenLockWarningAndSync) { window.top.HideScreenLockWarningAndSync(1080); } if(window.CMSContentManager) { CMSContentManager.allowSubmit = true; }; __doPostBack('ctl00$CMSPortalManager1$am',param); } function PM_Callback(param, callback, ctx) { if (window.top.HideScreenLockWarningAndSync) { window.top.HideScreenLockWarningAndSync(1080); }if (window.CMSContentManager) { CMSContentManager.storeContentChangedStatus(); };WebForm_DoCallback('ctl00$CMSPortalManager1$am',param,callback,ctx,null,true); } //]]> </script> <script src="/ScriptResource.axd?d=WTJtoz6EJe-loUBJ9stbRxqzgpVp8oo0KdZGkhGfcu6Lr7kb5LeNfx21FKi8mxEL1oDZOLAxiAqERpClgBx-A6lZ0DJ1qKcDZB1NuIbRd8o9S7aG0&t=7c776dc1" type="text/javascript"></script> <script src="/ScriptResource.axd?d=y6KGkkRaceYF_mkApXCXMQ_rMQVX59BlJ-ut-lQDHw88bR5bbS86epdVNwimj01duE6_OophLX4sBTOgb8_5dNLaY2Mx5DHMJj7Rbr4kPMV1-AOS5VF5-QEC8oG-_-aHoWoyqA2&t=7c776dc1" type="text/javascript"></script> <script type="text/javascript"> //<![CDATA[ var CMS = CMS || {}; CMS.Application = { "isDialog": false, "isDebuggingEnabled": false, "applicationUrl": "/", "isRTL": "false", "imagesUrl": "/CMSPages/GetResource.ashx?image=%5bImages.zip%5d%2f" }; //]]> </script> <div class="aspNetHidden"> <input type="hidden" name="__VIEWSTATEGENERATOR" id="__VIEWSTATEGENERATOR" value="AD1448C3" /> <input type="hidden" name="__EVENTVALIDATION" id="__EVENTVALIDATION" value="/wEdAAPQGCIHvXH59ixkmm2DXCEzDMN6QAizBz4KoPbUd79oAZD1NQdfl/cWuar5Vh7dGPS33XAgExACEKQwoobuEzLbtorwzg==" /> </div> <script type="text/javascript"> //<![CDATA[ Sys.WebForms.PageRequestManager._initialize('ctl00$manScript', 'aspnetForm', ['tctl00$ctxM',''], [], [], 90, 'ctl00'); //]]> </script> <div id="ctl00_ctxM"> </div> <header class="c-header"> <a href="#content" class="show-on-focus">Skip to main content</a> <div class="c-header-utilities"> <div class="container"> <div class="columns is-vcentered"> <div class="column"> <a href="https://asgct.org" class="is-external">ASGCT.org</a> </div> <div class="column is-half"> <a href="/"> <div class="c-header-images"> <div class="c-header-image"> <img src="/PatientEducation/media/PatientEducation/ASGCT_Web_Horz_Navy.png?ext=.png" alt="" /> </div> <div class="c-header-image"> <img src="/PatientEducation/media/PatientEducation/temp-pe-logo.png?ext=.png" alt="Patient Education Logo" /> </div> </div> </a> </div> <!--/search-results?searchtext=<enteredtext>--> <div class="column"> <div class="c-header-search"> <div class="c-header-search-wrap"> <input name="keyword" type="text" id="searchtext" placeholder="Search" aria-required="false" /> <label for="searchtext" class="is-sr-only">Keyword search</label> <button type="button" data-encode="searchtext" data-path="/search-results" data-query="searchtext"> <span class="is-sr-only">Search</span> <span class="c-search-icon"></span> </button> </div> </div> </div> </div> </div> </div> <div class="c-header-utilities-mobile"> <div class="c-header-images"> <div class="c-header-image"> <a href="https://asgct.org" class="is-external"><img src="/PatientEducation/media/PatientEducation/ASGCT_Web_Horz_Navy.png?ext=.png" alt="" /></a> </div> <div class="c-header-image"> <a href="/"><img src="/PatientEducation/media/PatientEducation/temp-pe-logo.png?ext=.png" alt="Patient Education Logo" /></a> </div> </div> <button class="c-nav-toggle" type="button" aria-controls="c-nav-main" aria-expanded="false" data-togglevisibility="data-togglevisibility"> <p class="is-sr-only">Open Navigation</p> <p class="is-sr-only" aria-hidden="true">Close Navigation</p> <span class="c-nav-toggle-menu"></span> </button> </div> <div id="ctl00_plcMain_bkSiteHeader_headerBanner"> <div class="header-alert"> <div class="container"> <p id="ctl00_plcMain_bkSiteHeader_pBanner"><b><a href="https://patienteducation.asgct.org/newsletter/subscribe-to-the-patient-press">Subscribe today to ASGCT's patient-centered newsletter, The Patient Press!</a></b></p> </div> </div> </div> <nav class="c-nav-main" id="c-nav-main" aria-hidden="true"> <div class="container"> <div class="c-header-search is-hidden-desktop"> <div class="c-header-search-wrap"> <input name="" type="text" id="global-search" placeholder="Search" aria-required="false" /> <label for="global-search" class="is-sr-only">Keyword search</label> <button type="button" data-encode="global-search" data-path="/search-results" data-query="searchtext"> <span class="is-sr-only">Search</span> <span class="c-search-icon"></span> </button> </div> </div> <ul> <li> <a href="/gene-therapy-101">Gene & Cell Therapy 101</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/gene-therapy-101/gene-therapy-basics">Gene Therapy Basics</a> </li> <li> <a href="/gene-therapy-101/cell-therapy-basics">Cell Therapy Basics</a> </li> <li> <a href="/gene-therapy-101/gene-therapy-approaches">Gene Therapy Approaches</a> </li> <li> <a href="/gene-therapy-101/gene-editing">Gene Editing</a> </li> <li> <a href="/gene-therapy-101/clinical-trials">Clinical Trials</a> </li> <li> <a href="/gene-therapy-101/vectors-101">Vectors 101</a> </li> <li> <a href="/gene-therapy-101/glossary">Glossary</a> </li> <li> <a href="/gene-therapy-101/covid19-vaccines">COVID-19</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/disease-treatments">Condition Treatments</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/disease-treatments/fda-approved-cell-gene-therapy-products">FDA-Approved Cell & Gene Therapy Products</a> </li> <li> <a href="/disease-treatments/batten">Batten Disease</a> </li> <li> <a href="/disease-treatments/blood-disorders">Beta Thalassemia & Other Blood Disorders</a> </li> <li> <a href="/disease-treatments/leukodystrophy">CALD and MLD</a> </li> <li> <a href="/disease-treatments/car-t-basics">CAR-T Basics</a> </li> <li> <a href="/disease-treatments/fabry">Fabry Disease</a> </li> <li> <a href="/disease-treatments/gaucher-disease">Gaucher Disease</a> </li> <li> <a href="/disease-treatments/gm1-gangliosidosis">GM1 Gangliosidosis</a> </li> <li> <a href="/disease-treatments/gm2-tay-sachs-sandhoff">Tay-Sachs and Sandhoff Disease</a> </li> <li> <a href="/disease-treatments/hemophilia">Hemophilia</a> </li> <li> <a href="/disease-treatments/huntingtons-disease">Huntington's Disease</a> </li> <li> <a href="/disease-treatments/inherited-retinal-diseases">Inherited Retinal Diseases</a> </li> <li> <a href="/disease-treatments/mps">Mucopolysaccharidoses (MPS)</a> </li> <li> <a href="/disease-treatments/muscular-dystrophy">Muscular Dystrophy</a> </li> <li> <a href="/disease-treatments/pompe-disease">Pompe Disease</a> </li> <li> <a href="/disease-treatments/parkinsons-disease">Parkinson's Disease</a> </li> <li> <a href="/disease-treatments/sickle-cell-disease">Sickle Cell Disease</a> </li> <li> <a href="/disease-treatments/sma">Spinal Muscular Atrophy</a> </li> <li> <a href="/disease-treatments/wilson-disease">Wilson Disease</a> </li> <li> <a href="/disease-treatments/xlmtm">X-Linked Myotubular Myopathy</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/patient-journey">Patient Journey</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/patient-journey/identifying-a-genetic-disease">Identifying a Genetic Disease</a> </li> <li> <a href="/patient-journey/next-steps-with-a-diagnosis">Next Steps With a Diagnosis</a> </li> <li> <a href="/patient-journey/patient-focused-policy-positions">Patient-Focused Policy Positions</a> </li> <li> <a href="/patient-journey/stimulating-research">Stimulating Research</a> </li> <li> <a href="/patient-journey/considering-a-clinical-trial">Considering a Clinical Trial</a> </li> <li> <a href="/patient-journey/ethical-issues-germline-gene-editing">Ethical Issues: Germline Gene Editing</a> </li> <li> <a href="/patient-journey/ethical-issues-illegitimate-clinical-trials">Ethical Issues: Unproven Stem Cell Products</a> </li> <li> <a href="/patient-journey/gene-therapy-centers">Gene Therapy Centers</a> </li> <li> <a href="/patient-journey/clinical-trials-finder">Clinical Trials Finder</a> </li> <li> <a href="/patient-journey/on-demand">On Demand Webinars</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/newsletter">Newsletter</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/newsletter/subscribe-to-the-patient-press">Subscribe to The Patient Press</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/quick-takes">Quick Takes</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/quick-takes/focused-ultrasound-in-cell-and-gene-therapies">Focused Ultrasound in CGTs</a> </li> <li> <a href="/quick-takes/access-to-approved-cell-and-gene-therapies">Access to Approved CGTs</a> </li> <li> <a href="/quick-takes/informed-consent">Informed Consent</a> </li> <li> <a href="/quick-takes/state-of-the-field-cgt-highlights-and-approvals-20">State of the Field: CGT Highlights and Approvals of 2023</a> </li> <li> <a href="/quick-takes/genetic-testing-and-clinical-trial-eligibility">Genetic Testing and Clinical Trial Eligibility</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/events">Events</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/events/empowering-patients-2025-a-cell-and-gene-therapies">Empowering Patients 2025: A Cell and Gene Therapies Summit</a> </li> <li> <a href="/events/annual-meeting-patient-advocate-offerings">Annual Meeting-Patient Advocate Offerings</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/about-asgct">About</a> <button type="button"><span class="is-sr-only">toggle subnavigation</span></button> <ul> <li> <a href="/about-asgct/overview">Overview</a> </li> <li> <a href="/about-asgct/about-asgct">About ASGCT</a> </li> <li> <a href="/about-asgct/news">ASGCT News</a> </li> <li> <a href="/about-asgct/privacy-policy">Privacy Policy</a> </li> </ul> <div class="navDropToggle"></div> </li> <li> <a href="/support">Support</a> </li> </ul> <a href="asgct.org" class="px-1 is-external is-hidden-desktop">ASGCT.org</a> </div> </nav> </header> <main class="c-main" id="content"> <section class="c-breadcrumbs"> <div class="container"> <span><a href="/">Home</a> > </span> <a href="/patient-journey" title="Patient Journey" class="CMSBreadCrumbsLink">Patient Journey</a> > <span class="CMSBreadCrumbsCurrentItem">Gene Therapy Centers</span> </div> </section> <section class="section"> <div class="container"> <div class="columns"> <div class="column is-8"> <h1 class="is-like-h2">Gene Therapy Centers</h1> </div> </div> <div class="columns"> <div class="column is-8"> <div class="c-leader"> </div> <div class="content mb-6"> <p>This list of gene therapy centers in the U.S. is intended for use by patients, advocates, and caregivers who are seeking gene therapy research for a rare disease. This list excludes oncology (cancer) due to the wide scope of cancers and number of centers working on them. The Blood & Marrow Transplant Information Network has <a href="https://www.bmtinfonet.org/transplant-article/medical-centers-offering-car-t-cell-therapy" target="_blank">a list of medical centers</a> offering CAR T-cell therapy. If you are unsure whether a clinical trial is open for your disease, search by diagnosis using the <a href="https://asgct.careboxhealth.com/" target="_blank">ASGCT Clinical Trials Finder</a>. To suggest a center or make an update to a center listed please <a href="mailto:akujawski@asgct.org">contact us</a>.</p> <table aria-rowcount="22" border="1" cellpadding="5" cellspacing="5" data-tablelook="1184" data-tablestyle="MsoTableGrid"> <tbody> <tr aria-rowindex="1" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{ed26f0d2-38aa-42ea-8481-679fd456c4d7}{224}" paraid="513201792" style="text-align: center;"><strong>Center </strong></p> <p paraeid="{ed26f0d2-38aa-42ea-8481-679fd456c4d7}{230}" paraid="400744358" style="text-align: center;"> </p> </td> <td data-celllook="0" role="columnheader"> <p paraeid="{ed26f0d2-38aa-42ea-8481-679fd456c4d7}{235}" paraid="1325133506" style="text-align: center;"><strong>Disease focus area* </strong></p> <p paraeid="{ed26f0d2-38aa-42ea-8481-679fd456c4d7}{245}" paraid="802611393" style="text-align: center;"> </p> </td> <td data-celllook="0" role="columnheader"> <p paraeid="{ed26f0d2-38aa-42ea-8481-679fd456c4d7}{250}" paraid="700922679" style="text-align: center;"><strong>Location </strong></p> </td> <td data-celllook="0" role="columnheader"> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{2}" paraid="6179727" style="text-align: center;"><strong>Contact </strong></p> </td> </tr> <tr aria-rowindex="2" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{10}" paraid="620284733"><strong>Boston Children’s Hospital Gene Therapy Program </strong></p> </td> <td data-celllook="0"> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{17}" paraid="804438684"><a href="https://www.childrenshospital.org/conditions/adrenoleukodystrophy-ald" rel="noreferrer noopener" target="_blank">adrenoleukodystrophy (ALD)</a> </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{25}" paraid="253796463">beta <a href="https://www.childrenshospital.org/conditions/thalassemia" rel="noreferrer noopener" target="_blank">thalassemia</a> </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{35}" paraid="1907849707"><a href="https://www.childrenshospital.org/conditions/hemophilia" rel="noreferrer noopener" target="_blank">hemophilia</a> A and B </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{45}" paraid="650978313"><a href="https://www.childrenshospital.org/conditions/inherited-retinal-disorders" rel="noreferrer noopener" target="_blank">inherited retinal disorders</a> </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{53}" paraid="653009893">ornithine transcarbamylase (OTC) deficiency </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{64}" paraid="1277807520"><a href="https://www.childrenshospital.org/conditions/sickle-cell-disease" rel="noreferrer noopener" target="_blank">sickle cell disease</a> </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{72}" paraid="2054530366"><a href="https://www.childrenshospital.org/conditions/spinal-muscular-atrophy-sma" rel="noreferrer noopener" target="_blank">spinal muscular atrophy (SMA)</a> </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{80}" paraid="240205786"><a href="https://www.childrenshospital.org/conditions/wiskott-aldrich-syndrome" rel="noreferrer noopener" target="_blank">Wiskott-Aldrich syndrome</a> </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{90}" paraid="1577793863">X-linked <a href="https://www.childrenshospital.org/conditions/severe-combined-immunodeficiency" rel="noreferrer noopener" target="_blank">severe combined immunodeficiency</a> (SCID-X1) </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{102}" paraid="1872839587">X-linked <a href="https://www.childrenshospital.org/conditions/chronic-granulomatous-disease-cgd" rel="noreferrer noopener" target="_blank">chronic granulomatous disease</a> (X-CGD) </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{114}" paraid="1358883256">relapsed or treatment-resistant B-cell <a href="https://www.childrenshospital.org/conditions/acute-lymphoblastic-leukemia-all" rel="noreferrer noopener" target="_blank">acute lymphoblastic leukemia (ALL)</a> </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{126}" paraid="2006562158">relapsed or refractory <a href="https://www.childrenshospital.org/conditions/large-cell-lymphoma" rel="noreferrer noopener" target="_blank">large B-cell lymphoma</a> </p> </td> <td data-celllook="0"> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{137}" paraid="158246645">Boston Children’s Hospital </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{143}" paraid="1590831035">300 Longwood Avenue, Boston MA 02115 </p> </td> <td data-celllook="0"> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{150}" paraid="548074149"><a href="tel:617-919-1992" rel="noreferrer noopener" target="_blank">617-919-1992</a> </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{157}" paraid="1061890814"><a href="https://www.childrenshospital.org/programs/gene-therapy-program" rel="noreferrer noopener" target="_blank">https://www.childrenshospital.org/programs/gene-therapy-program</a> </p> </td> </tr> <tr aria-rowindex="3" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{166}" paraid="263913563"><strong>Cell and Gene Therapy Collaborative at CHOP </strong></p> </td> <td data-celllook="0"> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{173}" paraid="261613082">Beta thalassemia </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{183}" paraid="1365454327">Choroideremia </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{189}" paraid="1692873023">Hemophilia </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{195}" paraid="341391845">Leber congenital amaurosis (LCA) </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{215}" paraid="1041158469">Methylmalonic acidemia </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{227}" paraid="2091966129">Mucopolysaccharidosis (MPS I, MPS II) </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{247}" paraid="1909895580">Phenylketonurias (PKU) </p> <p paraeid="{db9da3a6-26aa-4bf0-bbc4-25cd2dc95bd6}{255}" paraid="1416142774">Sickle cell disease </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{14}" paraid="1393133573">Spinal muscular atrophy (SMA) </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{30}" paraid="1194099127"> </p> </td> <td data-celllook="0"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{35}" paraid="1300989312">The Children’s Hospital of Philadelphia </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{41}" paraid="2089640052">3501 Civic Center Blvd </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{47}" paraid="124040157">Philadelphia, PA 19104 </p> </td> <td data-celllook="0"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{54}" paraid="1102992152"><a href="https://www.chop.edu/centers-programs/cell-and-gene-therapy-collaborative/contact-0" rel="noreferrer noopener" target="_blank">Contact</a> </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{63}" paraid="1861654103"><a href="https://www.chop.edu/centers-programs/cell-and-gene-therapy-collaborative" rel="noreferrer noopener" target="_blank">Learn more</a> </p> </td> </tr> <tr aria-rowindex="4" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{72}" paraid="1755317933"><strong>Cell and Gene Therapy Center at RowanSOM / Cooper Hospital</strong> </p> </td> <td data-celllook="0"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{83}" paraid="1923683083">Canavan disease </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{89}" paraid="904076432">Neurological disorders </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{99}" paraid="2135311232"> </p> </td> <td data-celllook="0"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{104}" paraid="743419104">Rowan University, School of Osteopathic Medicine </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{110}" paraid="794519490">2 Medical Center Drive, Science Center #253 </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{116}" paraid="1248686360">Stratford, NJ 08084 </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{122}" paraid="304778751"> </p> </td> <td data-celllook="0"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{127}" paraid="378997440">P: (856) 566-6334 </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{133}" paraid="998518779"><a href="mailto:leonepa@rowan.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{140}" paraid="1286919368"><a href="https://research.rowan.edu/research-areas/biomedical/leone/index.html" rel="noreferrer noopener" target="_blank">Learn more</a> </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{147}" paraid="960622557"> </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{151}" paraid="1084120670"> </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{155}" paraid="117661569"> </p> </td> </tr> <tr aria-rowindex="5" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{161}" paraid="377404605"><strong>Center for Cell and Gene Therapy at Baylor College of Medicine </strong></p> </td> <td data-celllook="0"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{170}" paraid="1355096517">AIDS </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{176}" paraid="367841381">Cardiovascular disease </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{182}" paraid="240515187"> </p> </td> <td data-celllook="0"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{187}" paraid="1603371143">Baylor College of Medicine <br /> One Baylor Plaza, Rm N1002 <br /> Houston, TX 77030 <br /> </p> </td> <td data-celllook="0"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{198}" paraid="1104147118">P: (832) 824-4670 </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{204}" paraid="1637729687"><a href="mailto:cagt@bcm.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{211}" paraid="107081804"><a href="https://www.bcm.edu/academic-centers/cell-and-gene-therapy" rel="noreferrer noopener" target="_blank">Learn more</a> </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{218}" paraid="1796837335"> </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{222}" paraid="1447291991"> </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{226}" paraid="707977556"> </p> </td> </tr> <tr aria-rowindex="6" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{232}" paraid="634918064"><strong>Center for Cell Engineering at Memorial Sloan Kettering Cancer Center </strong></p> </td> <td data-celllook="0"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{239}" paraid="1296131366">Blood disorders </p> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{245}" paraid="1839098673">Neurologic diseases </p> </td> <td data-celllook="0"> <p paraeid="{674b9840-8411-4baf-95b6-eaa84e936f70}{252}" paraid="1904422153">Center for Cell Engineering <br /> Memorial Sloan Kettering Cancer Center, Box 182 <br /> 1275 York Avenue <br /> New York, NY 10065 </p> </td> <td data-celllook="0"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{10}" paraid="2119942494"> </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{14}" paraid="1666641292">P: (212) 639-6394 </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{22}" paraid="1348707426">Email: <a href="mailto:becharde@mskcc.org" rel="noreferrer noopener" target="_blank">becharde@mskcc.org</a> </p> </td> </tr> <tr aria-rowindex="7" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{35}" paraid="1880875538"><strong>Department of Genetics and Genomic Sciences at Mount Sinai</strong> </p> </td> <td data-celllook="0"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{42}" paraid="804470407">Alzheimer's disease </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{50}" paraid="966246596">Cardiovascular illness </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{60}" paraid="1042834954">Crohn's disease </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{68}" paraid="658170126">Diabetes </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{74}" paraid="664483863">Infectious diseases </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{82}" paraid="2131691025">Lysosomal storage disorders </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{96}" paraid="725290171">Psychiatric illnesses </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{106}" paraid="1246820608">Ulcerative colitis </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{116}" paraid="2127224313"> </p> </td> <td data-celllook="0"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{121}" paraid="434577236">One Gustave L. Levy Place <br /> Box 1498 <br /> New York, NY 10029 </p> </td> <td data-celllook="0"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{132}" paraid="412279592">P: (212) 659-8542 </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{138}" paraid="1785855639"><a href="mailto:iigmbadmin@mssm.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{145}" paraid="687489776"><a href="https://icahn.mssm.edu/research/genomics" rel="noreferrer noopener" target="_blank">Learn more</a> </p> </td> </tr> <tr aria-rowindex="8" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{154}" paraid="499973931"><strong>Department of Microbiology & Molecular Genetics </strong></p> </td> <td data-celllook="0"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{161}" paraid="1373734915">Cystic fibrosis </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{169}" paraid="1248598455">Cardiovascular disease </p> </td> <td data-celllook="0"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{176}" paraid="605971223">University of Pittsburgh </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{182}" paraid="1020013138">523 Bridgeside Point II </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{192}" paraid="2139115973">450 Technology Drive </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{198}" paraid="2026759534">Pittsburgh, PA 15219 </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{204}" paraid="936765362"> </p> </td> <td data-celllook="0"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{209}" paraid="1108300325">P: (412) 648-9570 </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{215}" paraid="928450757"><a href="mailto:webmaster@mmg.pitt.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{222}" paraid="1487133888"><a href="http://www.mmg.pitt.edu/" rel="noreferrer noopener" target="_blank">Learn more</a> </p> </td> </tr> <tr aria-rowindex="9" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{231}" paraid="1694654464"><strong>Gene Therapy Program at UPenn </strong></p> </td> <td data-celllook="0"> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{238}" paraid="2048755854">Blood diseases </p> <p paraeid="{7d12a690-9604-45ab-93dd-0193f368cc53}{248}" paraid="977134298">Eye disorders </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{1}" paraid="1551950199">Infectious diseases </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{9}" paraid="1053748480">Lung diseases </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{17}" paraid="754110432">Metabolic diseases </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{25}" paraid="1863618606">Neurologic diseases </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{33}" paraid="1489768396">Neuromuscular disorders </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{41}" paraid="1979839521">Renal/liver diseases </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{53}" paraid="199320626"> </p> </td> <td data-celllook="0"> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{58}" paraid="233281622">Suite 1200 Translational Research Labs (TRL) </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{64}" paraid="147577334">125 S. 31st Street </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{70}" paraid="400747050">Philadelphia, PA 19104 </p> </td> <td data-celllook="0"> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{81}" paraid="2053341482">P: (215) 898-1281 </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{87}" paraid="201184568"><a href="mailto:psom-gtpadmin@pobox.upenn.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{94}" paraid="967218230"><a href="https://gtp.med.upenn.edu/" rel="noreferrer noopener" target="_blank">Learn more</a> </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{101}" paraid="1231863975"> </p> </td> </tr> <tr aria-rowindex="10" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{107}" paraid="2113694131"><strong>Grousbeck Gene Therapy Center </strong></p> </td> <td data-celllook="0"> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{116}" paraid="2001203333">Blindness </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{124}" paraid="337553676">Deafness </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{132}" paraid="761606393">Neurosensory disorders </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{142}" paraid="871236403">Other </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{148}" paraid="1676495339">Gene Delivery Technology Development </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{154}" paraid="2139925098"> </p> </td> <td data-celllook="0"> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{159}" paraid="637648626">MEE/SERI – 2W </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{165}" paraid="738657180">20 Stanford Street </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{171}" paraid="606227525">Boston, MA 02114 </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{177}" paraid="2099070383"> </p> </td> <td data-celllook="0"> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{182}" paraid="1765740677">P: (617)-573-6307 </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{188}" paraid="1404078126"><a href="mailto:luk_vandenberghe@meei.harvard.edu" rel="noreferrer noopener" target="_blank">Email direct</a> </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{199}" paraid="1617363931"><a href="mailto:aisling_ryan@meei.harvard.edu" rel="noreferrer noopener" target="_blank">Email admin</a> </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{212}" paraid="1317425470"><a href="https://www.vdb-lab.org/" rel="noreferrer noopener" target="_blank">Learn more</a> </p> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{219}" paraid="346667644"> </p> </td> </tr> <tr aria-rowindex="11" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{225}" paraid="1748989509"><strong>Horae Gene Therapy Center </strong></p> </td> <td data-celllook="0"> <p paraeid="{5c49578b-8e8f-4abb-9e99-1b7e5a87be1b}{232}" paraid="575401665">Alpha-1 Antitrypsin Deficiency <br /> Canavan disease <br /> Huntington's disease <br /> Inherited and acquired cardiac arrhythmias <br /> Leber congenital amaurosis (LCA) <br /> Lou Gehrig's disease (ALS) <br /> Neurofibromatosis Type 2 <br /> Retinitis pigmentosa <br /> Stargardt disease <br /> Tay-Sachs and Sandhoff disease </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{11}" paraid="1444094912">VLCAD Deficiency </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{17}" paraid="650178944"> </p> </td> <td data-celllook="0"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{22}" paraid="1185037559">UMass Medical School </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{28}" paraid="334324096">368 Plantation Street Worcester, MA 01605 </p> </td> <td data-celllook="0"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{39}" paraid="226263702">P: (508) 856-3394 </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{49}" paraid="766523752"><a href="mailto:Denise.Maclachlan@umassmed.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{56}" paraid="1728147580"><a href="https://www.umassmed.edu/gtc/" rel="noreferrer noopener" target="_blank">Learn more</a> </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{65}" paraid="1645568456"> </p> </td> </tr> <tr aria-rowindex="12" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{71}" paraid="584003016"><strong>IU School of Medicine Brown Center for Immunotherapy</strong> </p> </td> <td data-celllook="0"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{80}" paraid="1695021541">Alzheimer’s disease </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{86}" paraid="18618775"> </p> </td> <td data-celllook="0"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{91}" paraid="772700088">Walther Hall <br /> 980 W. Walnut Street <br /> Indianapolis, IN 46202 <br /> </p> </td> <td data-celllook="0"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{102}" paraid="2025546701">P: (317) 278-6969 </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{108}" paraid="1206949504"><a href="https://medicine.iu.edu/research-centers/immunotherapy" rel="noreferrer noopener" target="_blank">Learn more</a> </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{115}" paraid="2081659576"> </p> </td> </tr> <tr aria-rowindex="13" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{121}" paraid="1037848881"><strong>Mathews Center for Cellular Therapy </strong></p> </td> <td data-celllook="0"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{128}" paraid="1373136340">Adult stem cell transplant </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{134}" paraid="1300460530">Allergy and immunology </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{142}" paraid="1485158731">Solid organ transplant </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{150}" paraid="387016628"> </p> </td> <td data-celllook="0"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{155}" paraid="1662079956">Northwestern Memorial Hospital </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{161}" paraid="1621861849">710 N. Fairbanks Court </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{169}" paraid="505348489">Rm 7-613 </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{175}" paraid="1140688563">Chicago, IL 60611 </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{181}" paraid="915111638"> </p> </td> <td data-celllook="0"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{186}" paraid="205121194">P: (312) 926-2210 </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{192}" paraid="649312953"><a href="mailto:fenlu.zhu@nm.org" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{199}" paraid="778471474"><a href="https://www.nm.org/locations/mathews-center-for-cellular-therapy" rel="noreferrer noopener" target="_blank">Learn more</a> </p> </td> </tr> <tr aria-rowindex="14" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{208}" paraid="242008939"><strong>Nationwide Children’s Center for Gene Therapy </strong> </p> </td> <td data-celllook="0"> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{217}" paraid="1507281548">Infectious Diseases </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{229}" paraid="410259109">Ischemia </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{235}" paraid="1675713323">Lysosomal storage disorders </p> <p paraeid="{38d2fbcc-fcab-4676-a707-ffa4380fcc50}{251}" paraid="1299862215">Neuromuscular disorders </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{6}" paraid="1183957005">Neurodegenerative diseases </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{16}" paraid="1527063356">Neonatal hypertension </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{24}" paraid="1502598445">Reperfusion injury </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{32}" paraid="199707007"> </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{36}" paraid="1465397702"> </p> </td> <td data-celllook="0"> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{41}" paraid="349420580">The Abigail Wexner Research Institute at Nationwide Children's Hospital </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{53}" paraid="434464788">Research Bldg. II </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{59}" paraid="1436240284">Columbus, OH 43205 </p> </td> <td data-celllook="0"> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{66}" paraid="256607995">P: (614) 722-5615 </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{72}" paraid="909270742"><a href="mailto:Amanda.speakman@nationwidechildrens.org" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{79}" paraid="215773739"><a href="https://www.nationwidechildrens.org/research/areas-of-research/center-for-gene-therapy" rel="noreferrer noopener" target="_blank">Learn more</a> </p> </td> </tr> <tr aria-rowindex="15" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{88}" paraid="166032789"><strong>Nemours Children’s Hospital - Central Florida </strong></p> </td> <td data-celllook="0"> <ul type="disc"> <li>Duchenne Muscular Dystrophy</li> <li>Spinal muscular atrophy (SMA)</li> </ul> </td> <td data-celllook="0"> <p>Nemours Children’s Hospital</p> <p>6535 Nemours Parkway, Orlando Florida 32827</p> </td> <td data-celllook="0"> <p><a data-auth="NotApplicable" data-linkindex="3" href="tel:(407)%20650-7715" rel="noopener noreferrer" target="_blank">(407) 650-7715</a></p> <p><a data-auth="NotApplicable" data-linkindex="4" href="https://protect-us.mimecast.com/s/6xbKCpYloNivn1PsPRbiq" rel="noopener noreferrer" target="_blank">https://www.nemours.org/services/neuromuscular-disorders.html</a></p> </td> </tr> <tr aria-rowindex="16" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{111}" paraid="338665925"><strong>Powell Gene Therapy Center </strong></p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{117}" paraid="1307902598"><strong>and </strong></p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{123}" paraid="1538466288"><strong>Powell Center for Rare Disease Research </strong></p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{131}" paraid="1161731475"> </p> </td> <td data-celllook="0"> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{136}" paraid="290698299">Cardiovascular diseases </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{144}" paraid="1589724971">Central nervous system disorders </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{164}" paraid="1151131438">Endocrine disorders </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{172}" paraid="1681267127">Eye diseases </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{180}" paraid="463615779">Inflammatory disorders </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{188}" paraid="1647561498">Metabolic disorders </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{196}" paraid="1592324764">Neuromuscular disorders </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{204}" paraid="903578305">Pulmonary diseases </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{214}" paraid="1633813853"> </p> </td> <td data-celllook="0"> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{219}" paraid="286050107">University of Florida </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{225}" paraid="174950692">Academic Research Building College of Medicine </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{235}" paraid="1347579531">1200 Newell Drive </p> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{243}" paraid="469119391">Gainesville, FL 32610 </p> </td> <td data-celllook="0"> <p paraeid="{da8a4ac7-6675-4ac1-ae17-013cc0581082}{252}" paraid="998924472"><a href="https://pgtc.med.ufl.edu/" rel="noreferrer noopener" target="_blank">Gene Therapy Center</a> </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{4}" paraid="1889774533">P: (352) 294-5171 </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{10}" paraid="1704237693"><a href="mailto:pgtc-webinfo@peds.ufl.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{17}" paraid="1695847751"> </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{21}" paraid="1564530849"><a href="https://raredisease.powellcenter.med.ufl.edu/about-us/" rel="noreferrer noopener" target="_blank">Center for Rare Disease Research</a> </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{28}" paraid="2121491901"><a href="mailto:byrneresearchteam@peds.ufl.edu" rel="noreferrer noopener" target="_blank">Email </a> </p> </td> </tr> <tr aria-rowindex="17" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{41}" paraid="1496882345"><strong>The Vaccine and Gene Therapy Institute at OHSU</strong> </p> </td> <td data-celllook="0"> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{48}" paraid="1973321069">AIDS </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{54}" paraid="1833903854">Chronic viral infection-associated diseases </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{62}" paraid="1038013915">Infectious diseases </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{72}" paraid="944482869">Infectious diseases of the elderly </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{80}" paraid="531201248">Newly emerging viral diseases </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{88}" paraid="1625575830"> </p> </td> <td data-celllook="0"> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{93}" paraid="1884820216">Oregon Health & Science University – West Campus </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{99}" paraid="2111610129">505 N.W. 185th Avenue </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{105}" paraid="327319923">Beaverton, OR 97006 </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{111}" paraid="1331347654"> </p> </td> <td data-celllook="0"> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{116}" paraid="1813001622">P: (503) 418-2700 </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{122}" paraid="1869439556"><a href="mailto:vgti@ohsu.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{129}" paraid="1228412768"><a href="https://www.ohsu.edu/vaccine-gene-therapy-institute" rel="noreferrer noopener" target="_blank">Learn more</a> </p> </td> </tr> <tr aria-rowindex="18" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{138}" paraid="1920302189"><strong>Tulane Center for Stem Cell Research & Regenerative Medicine </strong></p> </td> <td data-celllook="0"> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{145}" paraid="1862974952">New therapies for common diseases including stroke, and multiple sclerosis </p> </td> <td data-celllook="0"> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{156}" paraid="279764580">Tulane University School of Medicine </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{162}" paraid="1390169085">1430 Tulane Avenue </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{168}" paraid="1387999461">New Orleans, LA 70112 </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{174}" paraid="739554589"> </p> </td> <td data-celllook="0"> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{179}" paraid="11521586">P: 504-988-5800 </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{185}" paraid="793396543"><a href="https://medicine.tulane.edu/centers-institutes/stem-cell-research-regenerative-medicine" rel="noreferrer noopener" target="_blank">Learn more</a> </p> </td> </tr> <tr aria-rowindex="19" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{194}" paraid="1609544805"><strong>UNC Gene Therapy Center </strong></p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{200}" paraid="1542307668"> </p> </td> <td data-celllook="0"> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{205}" paraid="875636731">Eye disorders </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{211}" paraid="1401020482">Hemophilia </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{217}" paraid="1948470923">Muscular dystrophies </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{229}" paraid="1462482700">Neurological disorders (epilepsy) </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{241}" paraid="768457165">Neuropathic lysosomal storage diseases (MPS and Krabbe disease) </p> <p paraeid="{07b98b71-3586-4bfe-a4ec-9d05c3350035}{255}" paraid="1913083085"> </p> </td> <td data-celllook="0"> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{5}" paraid="752275953">University of North Carolina </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{11}" paraid="1212206608">7119 Thurston Bowles Bldg. </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{19}" paraid="2033059977">104 Manning Drive </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{25}" paraid="1980395512">Campus Box 7352 </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{31}" paraid="464534221">Chapel Hill, NC 27599 </p> </td> <td data-celllook="0"> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{38}" paraid="1517768720">P: 919-962-3285 </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{44}" paraid="587899261"><a href="mailto:carla_alston_horton@med.unc.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{51}" paraid="304136592"><a href="https://www.med.unc.edu/genetherapy/" rel="noreferrer noopener" target="_blank">Learn more</a> </p> </td> </tr> <tr aria-rowindex="20" role="row"> <td data-celllook="65536" role="rowheader"> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{60}" paraid="342705019"><strong>University of Iowa Gene Therapy Center </strong> </p> </td> <td data-celllook="0"> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{67}" paraid="764085857">Cystic fibrosis </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{73}" paraid="908615371">Central nervous system disorders </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{89}" paraid="1009483366">Diseases affecting muscle, </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{101}" paraid="1031899194">vessels, skin, the liver and the lungs </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{127}" paraid="1209217029"> </p> </td> <td data-celllook="0"> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{132}" paraid="544943187">Roy J. and Lucille A. Carver College of Medicine </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{138}" paraid="811613498">451 Newton Road </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{144}" paraid="1998168595">200 Medicine Admin. Building </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{154}" paraid="1022269011">Iowa City, IA 52242 </p> </td> <td data-celllook="0"> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{161}" paraid="1015310312"><a href="https://medicine.uiowa.edu/genetherapy/" rel="noreferrer noopener" target="_blank">Learn more</a> </p> </td> </tr> <tr aria-rowindex="21" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{185}" paraid="1893293274"><strong>University of Minnesota Gene Therapy Center </strong></p> </td> <td data-celllook="0"> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{192}" paraid="2044228539">Mucopolysaccharidoses (MPS) and related diseases </p> </td> <td data-celllook="0"> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{201}" paraid="1649686244">Medical School Department of Pediatrics </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{211}" paraid="580021243">2450 Riverside Avenue </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{217}" paraid="1715815741">6th Floor, East Building </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{223}" paraid="176034515">Delivery Code 8952A </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{229}" paraid="9635865">Minneapolis, MN 55454 </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{235}" paraid="1744812650"> </p> </td> <td data-celllook="0"> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{240}" paraid="264715153">P: (612) 624-3113 </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{246}" paraid="1595598407"><a href="mailto:whitley@umn.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{e539c90f-87c1-44f6-b7fe-8fe89c5b3055}{253}" paraid="1368313312"> </p> </td> </tr> <tr aria-rowindex="22" role="row"> <td data-celllook="0" role="rowheader"> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{4}" paraid="190860360"><strong>UT Southwestern Medical Center </strong></p> </td> <td data-celllook="0"> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{13}" paraid="1618315285">Central nervous system disorders </p> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{23}" paraid="401770762">Neurodegenerative diseases </p> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{29}" paraid="1317011028">Neuromuscular disorders </p> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{35}" paraid="178157381">Lysosomal storage disorders </p> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{41}" paraid="1546869704">Metabolic disorders </p> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{47}" paraid="961869050">Genetic epilepsies </p> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{53}" paraid="1836858700">Neurodevelopmental disorders </p> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{59}" paraid="140188163"> </p> </td> <td data-celllook="0"> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{64}" paraid="1408950446">UT Southwestern Medical Center </p> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{70}" paraid="110646772">5323 Harry Hines Blvd. </p> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{76}" paraid="704744673">Dallas, TX 75390 </p> </td> <td data-celllook="0"> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{87}" paraid="1797104489"><a href="mailto:Roxana.Ploski@UTSouthwestern.edu" rel="noreferrer noopener" target="_blank">Email</a> </p> <p paraeid="{e9ea8d64-32c6-495e-a4f2-6eacc46cf28f}{96}" paraid="411457670"><a href="https://www.utsouthwestern.edu/labs/gray/" rel="noreferrer noopener" target="_blank">Learn more</a> </p> </td> </tr> </tbody> </table> </div> </div> <div class="column is-4 pl-4"> <div class="c-nav-local-wrap"> <div class="asideBox"> <h3> Related Pages</h3> <hr class="is-secondary" /> <ul class="c-nav-local-list"> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/patient-journey/identifying-a-genetic-disease">Identifying a Genetic Disease</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/patient-journey/next-steps-with-a-diagnosis">Next Steps With a Diagnosis</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/patient-journey/patient-focused-policy-positions">Patient-Focused Policy Positions</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/patient-journey/stimulating-research">Stimulating Research</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/patient-journey/considering-a-clinical-trial">Considering a Clinical Trial</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/patient-journey/ethical-issues-germline-gene-editing">Ethical Issues: Germline Gene Editing</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/patient-journey/ethical-issues-illegitimate-clinical-trials">Ethical Issues: Unproven Stem Cell Products</a> </li> <li class="c-nav-local-item is-active"><a class="c-nav-local-link" href="/patient-journey/gene-therapy-centers">Gene Therapy Centers</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/patient-journey/clinical-trials-finder">Clinical Trials Finder</a> </li> <li class="c-nav-local-item"><a class="c-nav-local-link" href="/patient-journey/on-demand">On Demand Webinars</a> </li> </ul> </div> </div> </div> </div> </div> <div class="lastUpdatedTag"> <p>Last Updated: 11/07/2024</p> </div> </section> </main> <footer class="c-footer"> <div class="c-footer-primary"> <section class="section"> <div class="container"> <div class="columns"> <div class="column c-footer-section"> <p><img alt="" src="/PatientEducation/media/PatientEducation/logo_white.png" /></p> <p>20800 Swenson Dr., Suite 300<br /> Waukesha, WI 53186</p> </div> <div class="column is-two-fifths c-footer-section"> <ul class="c-utility-list"> <li><a href="#">Gene Therapy 101</a></li> <li><a href="#">Disease Treatments</a></li> <li><a href="#">Clinical Trials</a></li> <li><a href="/patient-journey">Patient Journey</a></li> <li><a href="/about-asgct">About</a></li> <li><a href="/support">Support</a></li> <li><a href="https://asgct.org/about/privacy-policy" target="_blank">Privacy Policy</a></li> </ul> </div> <div class="column c-footer-section"> <h3 class="mb-3">Connect with ASGCT</h3> <p class="mb-0"><span>Phone: 414</span>.278.1341</p> <p><a href="mailto:info@asgct.org">info@asgct.org</a></p> <p> <div class="c-social"> <ul class="c-social-list"> <li class="c-social-item"><a href="https://twitter.com/ASGCTherapy" target="_blank" class="c-social-link twitter"><span class="is-sr-only">Twitter</span></a></li> <li class="c-social-item"><a href="https://www.facebook.com/ASGCTherapy" target="_blank" class="c-social-link facebook"><span class="is-sr-only">Facebook</span></a></li> <li class="c-social-item"><a href="https://www.instagram.com/asgctherapy" target="_blank" class="c-social-link instagram"><span class="is-sr-only">Instagram</span></a></li> <li class="c-social-item"><a href="https://www.linkedin.com/company/asgct" target="_blank" class="c-social-link linkedin"><span class="is-sr-only">LinkedIn</span></a></li> <li class="c-social-item"><a href="https://www.youtube.com/user/ASGCT" target="_blank" class="c-social-link youtube"><span class="is-sr-only">YouTube</span></a></li> </ul> </div> </p> </div> </div> </div> </section> </div> <div class="c-footer-secondary"> <section class="section py-4"> <div class="container"> <div class="columns"> <div class="column"> <p class="is-small">© 2024 All rights reserved. American Society of Gene & Cell Therapy.</p> <p class="is-tiny">Web design by <a href="https://www.reasononeinc.com/kentico" target="_blank">Reason One</a>. Powered by <a href="http://www.kentico.com" target="_blank">Kentico</a>.</p> </div> </div> </div> </section> </div> </footer> <div class="CookieConsent"> <span id="ctl00_cookieLawQ_lblText" class="ConsentText">This site uses cookies to offer you a better user experience and to analyze site traffic. By continuing to use this website, you accept our use of cookies.</span> <span class="ConsentButtons"> <input type="submit" name="ctl00$cookieLawQ$btnAllowSpecific" value="OPT OUT" id="ctl00_cookieLawQ_btnAllowSpecific" class="ConsentButton btn btn-default" /> <input type="submit" name="ctl00$cookieLawQ$btnAllowAll" value="ACCEPT" id="ctl00_cookieLawQ_btnAllowAll" class="ConsentButton btn btn-default" /> </span> </div> <script src="/BlueKey/pe_assets/build/main.js" type="text/javascript"></script> <script type="text/javascript"> //<![CDATA[ var callBackFrameUrl='/WebResource.axd?d=nNME_ObE2oIDm535eYM9xWmIMy-HXBVdo54Ly6sA5tAYPS1aA-gFDzodlP9ijTBRgmjStONrH4-ISuRTp7slHiYkACw1&t=638562384440000000'; WebForm_InitCallback();//]]> </script> </form> </body> </html>