Gene & Cell Therapy 101 |

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class="navDropToggle"></div> </li> <li> <a href="/support">Support</a> </li> </ul> <a href="asgct.org" class="px-1 is-external is-hidden-desktop">ASGCT.org</a> </div> </nav> <div class="c-banner" style="background: url('/getattachment/Gene-Therapy-101/Batten_Disease_1280x720_3_00000.png.aspx') 50%/cover no-repeat;"> <div class="c-banner-content container"> <h1>Gene & Cell Therapy 101</h1> <hr /> <p class="is-large">Gene therapy can stop or slow the effects of disease on the most basic level of the human body鈥攐ur genes. Cell therapy is the transfer of a specific cell type(s) into a person to treat or prevent a disease. </p> </div> </div> </header> <main class="c-main" id="content"> <section class="section mb-6"> <div class="container"> <div class="c-cta c-cta-primary pt-6"> <div class="c-cta-wrap columns is-vcentered"> <div class="column is-5"> <div class="c-cta-content"> <h2>Gene Therapy Basics</h2> <p>Gene therapy is the use of genetic material in the treatment or prevention of disease.</p> <a href="/gene-therapy-102/gene-therapy-basics" class="c-button-secondary" target="_self">Learn More</a> </div> </div> <div class="column is-6 is-offset-1 is-centered"> <img src="/getattachment/Gene-Therapy-101/Test-Call-to-Action/Fabry_Disease_330x230_5_00000.png.aspx" alt="GT Basics" /> </div> </div> </div> </div> </section> <section class="section wrap"> <div class="container"> <div class="is-flex-center tile is-ancestor py-5"> <div class="tile is-6 is-parent"> <a href="/Gene-Therapy-101/Cell-Therapy-Basics" class="tile is-child c-tile-link-alternate"> <h2>Cell Therapy Basics</h2><p>Cell therapy is the transfer of a specific cell type(s) into a person to treat or prevent a disease.</p> </a> </div> <div class="tile is-6 is-parent"> <a href="/Gene-Therapy-102/Vectors-101" class="tile is-child c-tile-link-alternate"> <h2>Vectors 101</h2><p>Vectors are essentially vehicles designed to deliver therapeutic genetic material, such as a working gene, directly into a cell.</p> </a> </div> </div> </div> </section> <section class="section wrap pattern pb-x1" style="background: url('/PatientEducation/media/PatientEducation/square-background.png') repeat;"> <div class="container pt-6"> <div class="columns"> <div class="column is-three-fifths is-offset-one-fifth is-centered"> <h2>More Resources</h2> </div> </div> <div class="columns"> <div class="column is-10 is-offset-1"> <div class="c-tile-wrap mb-5"> <div class="c-tile"> <a href="/gene-therapy-101/gene-therapy-approaches" class="c-tile-link"> <h3>Gene Therapy Approaches</h3> <hr /> <p>Learn more about some common approaches that target the underlying problem.</p> </a> </div> <div class="c-tile"> <a href="/gene-therapy-101/clinical-trials" class="c-tile-link"> <h3>Clinical Trials</h3> <hr /> <p>How do clinical trials work? Here we learn about the process of developing a treatment.</p> </a> </div> <div class="c-tile"> <a href="/gene-therapy-101/gene-editing" class="c-tile-link"> <h3>Gene Editing</h3> <hr /> <p>Gene editing aims to be a one-time therapy that directly edits pieces of DNA within the cell.</p> </a> </div> <div class="c-tile"> <a href="/gene-therapy-101/glossary" class="c-tile-link"> <h3>Glossary</h3> <hr /> <p>Common terms in cell and gene therapy, from A-to-Z.</p> </a> </div> <div class="c-tile"> <a href="/gene-therapy-101/helpful-websites" class="c-tile-link"> <h3>Helpful Websites</h3> <hr /> <p>Visit these websites for more gene and cell therapy resources.</p> </a> </div> </div> </div> </div> </div> </section> </main> <footer class="c-footer"> <div class="c-footer-primary"> <section class="section"> <div class="container"> <div class="columns"> <div class="column c-footer-section"> <p><img alt="" src="/PatientEducation/media/PatientEducation/logo_white.png" /></p> <p>20800 Swenson Dr., Suite 300<br /> Waukesha, WI 53186</p> </div> <div class="column is-two-fifths c-footer-section"> <ul class="c-utility-list"> <li><a href="#">Gene Therapy 101</a></li> <li><a href="#">Disease Treatments</a></li> <li><a href="#">Clinical Trials</a></li> <li><a href="/patient-journey">Patient Journey</a></li> <li><a href="/about-asgct">About</a></li> <li><a href="/support">Support</a></li> <li><a href="https://asgct.org/about/privacy-policy" target="_blank">Privacy Policy</a></li> </ul> </div> <div class="column c-footer-section"> <h3 class="mb-3">Connect with ASGCT</h3> <p class="mb-0"><span>Phone: 414</span>.278.1341</p> <p><a href="mailto:info@asgct.org">info@asgct.org</a></p> <p> <div class="c-social"> <ul class="c-social-list"> <li class="c-social-item"><a href="https://twitter.com/ASGCTherapy" target="_blank" class="c-social-link twitter"><span class="is-sr-only">Twitter</span></a></li> <li class="c-social-item"><a href="https://www.facebook.com/ASGCTherapy" target="_blank" class="c-social-link facebook"><span class="is-sr-only">Facebook</span></a></li> <li class="c-social-item"><a href="https://www.instagram.com/asgctherapy" target="_blank" class="c-social-link instagram"><span class="is-sr-only">Instagram</span></a></li> <li class="c-social-item"><a href="https://www.linkedin.com/company/asgct" target="_blank" class="c-social-link linkedin"><span class="is-sr-only">LinkedIn</span></a></li> <li class="c-social-item"><a href="https://www.youtube.com/user/ASGCT" target="_blank" class="c-social-link youtube"><span class="is-sr-only">YouTube</span></a></li> </ul> </div> </p> </div> </div> </div> </section> </div> <div class="c-footer-secondary"> <section class="section py-4"> <div class="container"> <div class="columns"> <div class="column"> <p class="is-small">© 2024 All rights reserved. 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